| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy
|
Hakim, Chady H.
|
|
2017
|
6 |
C |
p. 216-230
15 p.
|
artikel
|
| 2 |
Anti-high Mobility Group Box 1 Antibody Ameliorates Albuminuria in MRL/lpr Lupus-Prone Mice
|
Watanabe, Haruki
|
|
2017
|
6 |
C |
p. 31-39
9 p.
|
artikel
|
| 3 |
Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice
|
Aoyagi-Scharber, Mika
|
|
2017
|
6 |
C |
p. 43-53
11 p.
|
artikel
|
| 4 |
Deletion of the Virion Host Shut-off Gene Enhances Neuronal-Selective Transgene Expression from an HSV Vector Lacking Functional IE Genes
|
Miyagawa, Yoshitaka
|
|
2017
|
6 |
C |
p. 79-90
12 p.
|
artikel
|
| 5 |
Generation of a Vero-Based Packaging Cell Line to Produce SV40 Gene Delivery Vectors for Use in Clinical Gene Therapy Studies
|
Toscano, Miguel G.
|
|
2017
|
6 |
C |
p. 124-134
11 p.
|
artikel
|
| 6 |
Global Screening of Antiviral Genes that Suppress Baculovirus Transgene Expression in Mammalian Cells
|
Wang, Chia-Hung
|
|
2017
|
6 |
C |
p. 194-206
13 p.
|
artikel
|
| 7 |
In Silico Restriction Enzyme Digests to Minimize Mapping Bias in Genomic Sequencing
|
Roszik, Jason
|
|
2017
|
6 |
C |
p. 66-67
2 p.
|
artikel
|
| 8 |
In Vivo Murine-Matured Human CD3+ Cells as a Preclinical Model for T Cell-Based Immunotherapies
|
Haworth, Kevin G.
|
|
2017
|
6 |
C |
p. 17-30
14 p.
|
artikel
|
| 9 |
Lentiviral Fluorescent Genetic Barcoding for Multiplex Fate Tracking of Leukemic Cells
|
Maetzig, Tobias
|
|
2017
|
6 |
C |
p. 54-65
12 p.
|
artikel
|
| 10 |
Lipidomic Evaluation of Feline Neurologic Disease after AAV Gene Therapy
|
Gray-Edwards, Heather L.
|
|
2017
|
6 |
C |
p. 135-142
8 p.
|
artikel
|
| 11 |
Long-Term Efficacy and Safety of Insulin and Glucokinase Gene Therapy for Diabetes: 8-Year Follow-Up in Dogs
|
Jaén, Maria Luisa
|
|
2017
|
6 |
C |
p. 1-7
7 p.
|
artikel
|
| 12 |
Mesenchymal Stem Cells Overexpressing Interleukin-10 Promote Neuroprotection in Experimental Acute Ischemic Stroke
|
Nakajima, Masataka
|
|
2017
|
6 |
C |
p. 102-111
10 p.
|
artikel
|
| 13 |
Minimal Purkinje Cell-Specific PCP2/L7 Promoter Virally Available for Rodents and Non-human Primates
|
Nitta, Keisuke
|
|
2017
|
6 |
C |
p. 159-170
12 p.
|
artikel
|
| 14 |
Neonatal Gene Therapy for Hemophilia B by a Novel Adenovirus Vector Showing Reduced Leaky Expression of Viral Genes
|
Iizuka, Shunsuke
|
|
2017
|
6 |
C |
p. 183-193
11 p.
|
artikel
|
| 15 |
Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI
|
Ferla, Rita
|
|
2017
|
6 |
C |
p. 143-158
16 p.
|
artikel
|
| 16 |
Public Attitudes toward Gene Therapy in China
|
Wang, Jiang-Hui
|
|
2017
|
6 |
C |
p. 40-42
3 p.
|
artikel
|
| 17 |
Regulatable Transgene Expression for Prevention of Chemotherapy-Induced Peripheral Neuropathy
|
Kawata, Daisuke
|
|
2017
|
6 |
C |
p. 91-101
11 p.
|
artikel
|
| 18 |
Safety and Efficacy of the Complement Inhibitor AMY-101 in a Natural Model of Periodontitis in Non-human Primates
|
Kajikawa, Tetsuhiro
|
|
2017
|
6 |
C |
p. 207-215
9 p.
|
artikel
|
| 19 |
Single Cell-Based Vector Tracing in Patients with ADA-SCID Treated with Stem Cell Gene Therapy
|
Igarashi, Yuka
|
|
2017
|
6 |
C |
p. 8-16
9 p.
|
artikel
|
| 20 |
Targeting Visceral Fat by Intraperitoneal Delivery of Novel AAV Serotype Vector Restricting Off-Target Transduction in Liver
|
Huang, Wei
|
|
2017
|
6 |
C |
p. 68-78
11 p.
|
artikel
|
| 21 |
Thermal Stability as a Determinant of AAV Serotype Identity
|
Bennett, Antonette
|
|
2017
|
6 |
C |
p. 171-182
12 p.
|
artikel
|
| 22 |
Traceless Targeting and Isolation of Gene-Edited Immortalized Keratinocytes from Epidermolysis Bullosa Simplex Patients
|
Aushev, Magomet
|
|
2017
|
6 |
C |
p. 112-123
12 p.
|
artikel
|
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