Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice
Titel:
Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice
Auteur:
Aoyagi-Scharber, Mika Crippen-Harmon, Danielle Lawrence, Roger Vincelette, Jon Yogalingam, Gouri Prill, Heather Yip, Bryan K. Baridon, Brian Vitelli, Catherine Lee, Amanda Gorostiza, Olivia Adintori, Evan G. Minto, Wesley C. Van Vleet, Jeremy L. Yates, Bridget Rigney, Sara Christianson, Terri M. Tiger, Pascale M.N. Lo, Melanie J. Holtzinger, John Fitzpatrick, Paul A. LeBowitz, Jonathan H. Bullens, Sherry Crawford, Brett E. Bunting, Stuart