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Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI |
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Titel: |
Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI |
Auteur: |
Ferla, Rita Alliegro, Marialuisa Marteau, Jean-Brice Dell’Anno, Margherita Nusco, Edoardo Pouillot, Severine Galimberti, Stefania Valsecchi, Maria Grazia Zuliani, Vincent Auricchio, Alberto |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 6 (2017) nr. C pagina's 16 p. |
Jaar: |
2017 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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