| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV9-mediated central nervous system–targeted gene delivery via cisterna magna route in mice
|
Lukashchuk, Vera
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 2 |
AAV-mediated Sirt1 overexpression in skeletal muscle activates oxidative capacity but does not prevent insulin resistance
|
Vil, Laia
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 3 |
A comparison of foamy and lentiviral vector genotoxicity in SCID-repopulating cells shows foamy vectors are less prone to clonal dominance
|
Everson, Elizabeth M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 4 |
All-in-one processing of heterogeneous human cell grafts for gene and cell therapy
|
Lukianova-Hleb, Ekaterina Y
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 5 |
An HSV-based library screen identifies PP1α as a negative TRPV1 regulator with analgesic activity in models of pain
|
Reinhart, Bonnie
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 6 |
A regulatable AAV vector mediating GDNF biological effects at clinically-approved sub-antimicrobial doxycycline doses
|
Chtarto, Abdelwahed
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 7 |
A scalable method for the production of high-titer and high-quality adeno-associated type 9 vectors using the HSV platform
|
Adamson-Small, Laura
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 8 |
Assessment of murine colorectal cancer by micro-ultrasound using three dimensional reconstruction and non-linear contrast imaging
|
Freeling, Jessica L
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 9 |
A targeted controlled force injection of genetic material in vivo
|
Ahlén, Gustaf
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 10 |
A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome
|
Ronzitti, Giuseppe
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 11 |
Biodistribution studies: understanding international expectations
|
Huang, Ying
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 12 |
Broad HIV-1 inhibition in vitro by vaccine-elicited CD8+ T cells in African adults
|
Mutua, Gaudensia
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 13 |
Clinical development of gene- and cell-based therapies: overview of the European landscape
|
de Wilde, Sofieke
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 14 |
Clinical development of gene therapy: results and lessons from recent successes
|
Kumar, Sandeep RP
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 15 |
Comparative study of human embryonic stem cells (hESC) and human induced pluripotent stem cells (hiPSC) as a treatment for retinal dystrophies
|
Riera, Marina
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 16 |
Constitutively active form of natriuretic peptide receptor 2 ameliorates experimental pulmonary arterial hypertension
|
Nawa, Nobutoshi
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 17 |
Construction of a hybrid β-hexosaminidase subunit capable of forming stable homodimers that hydrolyze GM2 ganglioside in vivo
|
Tropak, Michael B
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 18 |
Corrigendum to “Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho–/– mouse”
|
Palfi, Arpad
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 19 |
Design of a titering assay for lentiviral vectors utilizing direct extraction of DNA from transduced cells in microtiter plates
|
Murphy, Michele E
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 20 |
Development of a real-time imaging system for hypoxic cell apoptosis
|
Kagiya, Go
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 21 |
Distribution of AAV8 particles in cell lysates and culture media changes with time and is dependent on the recombinant vector
|
Piras, Bryan A
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 22 |
Dual therapeutic functions of F-5 fragment in burn wounds: preventing wound progression and promoting wound healing in pigs
|
Bhatia, Ayesha
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 23 |
Dynamics of antigen presentation to transgene product-specific CD4+ T cells and of Treg induction upon hepatic AAV gene transfer
|
Perrin, George Q
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 24 |
Effects of FVIII immunity on hepatocyte and hematopoietic stem cell–directed gene therapy of murine hemophilia A
|
Lytle, Allison M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 25 |
Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy
|
Armbruster, Nicole
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 26 |
Efficient detection of human circulating tumor cells without significant production of false-positive cells by a novel conditionally replicating adenovirus
|
Sakurai, Fuminori
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 27 |
Elimination of proliferating cells from CNS grafts using a Ki67 promoter-driven thymidine kinase
|
Tieng, Vannary
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 28 |
Expression mediated by three partial sequences of the human tyrosine hydroxylase promoter in vivo
|
Rolland, Anne-Sophie
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 29 |
Ex vivo expansion of circulating CD34+ cells enhances the regenerative effect on rat liver cirrhosis
|
Nakamura, Toru
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 30 |
Fbxw7-associated drug resistance is reversed by induction of terminal differentiation in murine intestinal organoid culture
|
Lorenzi, Federica
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 31 |
100-fold but not 50-fold dystrophin overexpression aggravates electrocardiographic defects in the mdx model of Duchenne muscular dystrophy
|
Yue, Yongping
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 32 |
From selection hits to clinical leads: progress in aptamer discovery
|
Maier, Keith E
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 33 |
Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery
|
Fu, Haiyan
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 34 |
Helper virus-mediated downregulation of transgene expression permits production of recalcitrant helper-dependent adenoviral vector
|
Palmer, Donna J
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 35 |
Impact of age and vector construct on striatal and nigral transgene expression
|
Polinski, Nicole K
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 36 |
Impact of intravenous infusion time on AAV8 vector pharmacokinetics, safety, and liver transduction in cynomolgus macaques
|
Greig, Jenny A
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 37 |
In utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical application
|
Almeida-Porada, Graça
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 38 |
Investigating the functionality of an OCT4-short response element in human induced pluripotent stem cells
|
Vega-Crespo, Agustin
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 39 |
Manufacturing of AcMNPV baculovirus vectors to enable gene therapy trials
|
Kwang, Timothy Weixin
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 40 |
Manufacturing of recombinant adeno-associated viral vectors for clinical trials
|
Clément, Nathalie
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 41 |
Manufacturing of recombinant adeno-associated viral vectors: new technologies are welcome
|
Ayuso, Eduard
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 42 |
“Marker of Self” CD47 on lentiviral vectors decreases macrophage-mediated clearance and increases delivery to SIRPA-expressing lung carcinoma tumors
|
Sosale, Nisha G
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 43 |
Merging DBS with viral vector or stem cell implantation: “hybrid” stereotactic surgery as an evolution in the surgical treatment of Parkinson's disease
|
Rowland, Nathan C
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 44 |
Methods and clinical development of adenovirus-vectored vaccines against mucosal pathogens
|
Afkhami, Sam
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 45 |
Microglia-specific targeting by novel capsid-modified AAV6 vectors
|
Rosario, Awilda M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 46 |
Moving oncolytic viruses into the clinic: clinical-grade production, purification, and characterization of diverse oncolytic viruses
|
Ungerechts, Guy
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 47 |
Moving toward a higher efficiency of microcell-mediated chromosome transfer
|
Liskovykh, Mikhail
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 48 |
Multilineage polyclonal engraftment of Cal-1 gene-modified cells and in vivo selection after SHIV infection in a nonhuman primate model of AIDS
|
Peterson, Christopher W.
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 49 |
Multilineage transduction of resident lung cells in vivo by AAV2/8 for α1-antitrypsin gene therapy
|
Payne, Julia G
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 50 |
Multiple mechanisms determine the sensitivity of human-induced pluripotent stem cells to the inducible caspase-9 safety switch
|
Yagyu, Shigeki
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 51 |
Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice
|
Marangoni, Dario
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 52 |
Overexpression of factor VIII after AAV delivery is transiently associated with cellular stress in hemophilia A mice
|
Lange, Amy M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 53 |
PAX6 MiniPromoters drive restricted expression from rAAV in the adult mouse retina
|
Hickmott, Jack W
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 54 |
Plasma-activated air mediates plasmid DNA delivery in vivo
|
Edelblute, Chelsea M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 55 |
Potential for cellular stress response to hepatic factor VIII expression from AAV vector
|
Zolotukhin, Irene
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 56 |
Potent spinal parenchymal AAV9-mediated gene delivery by subpial injection in adult rats and pigs
|
Miyanohara, Atsushi
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 57 |
Practical utilization of recombinant AAV vector reference standards: focus on vector genomes titration by free ITR qPCR
|
D'Costa, Susan
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 58 |
Preclinical development and qualification of ZFN-mediated CCR5 disruption in human hematopoietic stem/progenitor cells
|
DiGiusto, David L
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 59 |
Preclinical evaluation of mesenchymal stem cells overexpressing VEGF to treat critical limb ischemia
|
Beegle, Julie R
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 60 |
Preclinical safety, pharmacokinetics, pharmacodynamics, and biodistribution studies with Ad35K++ protein: a novel rituximab cotherapeutic
|
Richter, Maximilian
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 61 |
Preclinical validation: LV/IL-12 transduction of patient leukemia cells for immunotherapy of AML
|
Huang, Ju
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 62 |
Production and clinical development of nanoparticles for gene delivery
|
Chen, Jie
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 63 |
Production and purification of high-titer foamy virus vector for the treatment of leukocyte adhesion deficiency
|
Nasimuzzaman, Md
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 64 |
Production of lentiviral vectors
|
Merten, Otto-Wilhelm
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 65 |
Promise and problems associated with the use of recombinant AAV for the delivery of anti-HIV antibodies
|
Fuchs, Sebastian P
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 66 |
Prophylactic and therapeutic adenoviral vector-based multivirus-specific T-cell immunotherapy for transplant patients
|
Dasari, Vijayendra
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 67 |
Protein transduction therapy into cochleae via the round window niche in guinea pigs
|
Takeda, Hiroki
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 68 |
Purification of baculovirus vectors using heparin affinity chromatography
|
Nasimuzzaman, Md
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 69 |
Quantification of designer nuclease induced mutation rates: a direct comparison of different methods
|
Ehrke-Schulz, Eric
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 70 |
Rapid cloning, expression, and functional characterization of paired αβ and γδ T-cell receptor chains from single-cell analysis
|
Guo, Xi-zhi J
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 71 |
Rapid, scalable, and low-cost purification of recombinant adeno-associated virus produced by baculovirus expression vector system
|
Buclez, Pierre-Olivier
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 72 |
RD-MolPack technology for the constitutive production of self-inactivating lentiviral vectors pseudotyped with the nontoxic RD114-TR envelope
|
Marin, Virna
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 73 |
Retinal pigment epithelial cell expression of active Rap 1a by scAAV2 inhibits choroidal neovascularization
|
Wang, Haibo
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 74 |
Robust generation of transgenic mice by simple hypotonic solution mediated delivery of transgene in testicular germ cells
|
Usmani, Abul
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 75 |
Safety and biodistribution assessment of sc-rAAV2.5IL-1Ra administered via intra-articular injection in a mono-iodoacetate-induced osteoarthritis rat model
|
Wang, Gensheng
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 76 |
Sendai virus, an RNA virus with no risk of genomic integration, delivers CRISPR/Cas9 for efficient gene editing
|
Park, Arnold
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 77 |
Significant changes in endogenous retinal gene expression assessed 1 year after a single intraocular injection of AAV-CNTF or AAV-BDNF
|
LeVaillant, Chrisna J
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 78 |
Strategies to generate high-titer, high-potency recombinant AAV3 serotype vectors
|
Ling, Chen
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 79 |
Tailored transgene expression to specific cell types in the central nervous system after peripheral injection with AAV9
|
Dashkoff, Jonathan
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 80 |
Targeted approaches to induce immune tolerance for Pompe disease therapy
|
Doerfler, Phillip A
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 81 |
TFEB overexpression promotes glycogen clearance of Pompe disease iPSC-derived skeletal muscle
|
Sato, Yohei
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 82 |
The feasibility of incorporating Vpx into lentiviral gene therapy vectors
|
McAllery, Samantha A
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 83 |
The identification of hematopoietic-specific regulatory elements for WASp gene expression
|
Zhan, Jun
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 84 |
The impact of minimally oversized adeno-associated viral vectors encoding human factor VIII on vector potency in vivo
|
Kyostio-Moore, Sirkka
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 85 |
The superior regenerative potential of muscle-derived stem cells for articular cartilage repair is attributed to high cell survival and chondrogenic potential
|
Li, Hongshuai
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 86 |
Total body irradiation must be delivered at high dose for efficient engraftment and tolerance in a rhesus stem cell gene therapy model
|
Uchida, Naoya
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 87 |
Towards routine manufacturing of gene therapy drugs
|
Merten, Otto-Wilhelm
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 88 |
Transcriptional activity of novel ALDH1L1 promoters in the rat brain following AAV vector-mediated gene transfer
|
Mudannayake, Janitha M
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 89 |
Transcriptionally regulated and nontoxic delivery of the hyperactive Sleeping Beauty Transposase
|
Cocchiarella, Fabienne
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 90 |
Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector
|
Nakamura-Takahashi, Aki
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 91 |
Treatment of osteoarthritis using a helper-dependent adenoviral vector retargeted to chondrocytes
|
Ruan, Merry ZC
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 92 |
Ultracentrifugation-free chromatography-mediated large-scale purification of recombinant adeno-associated virus serotype 1 (rAAV1)
|
Tomono, Taro
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 93 |
Viral-mediated Ntf3 overexpression disrupts innervation and hearing in nondeafened guinea pig cochleae
|
Lee, Min Young
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
| 94 |
Widespread AAV1- and AAV2-mediated transgene expression in the nonhuman primate brain: implications for Huntington's disease
|
Hadaczek, Piotr
|
|
2016
|
3 |
C |
p. -
1 p.
|
artikel
|
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