Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice
Titel:
Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice
Auteur:
Marangoni, Dario Bush, Ronald A Zeng, Yong Wei, Lisa L Ziccardi, Lucia Vijayasarathy, Camasamudram Bartoe, Joshua T Palyada, Kiran Santos, Maria Hiriyanna, Suja Wu, Zhijian Colosi, Peter Sieving, Paul A
Verschenen in:
Molecular therapy. Methods & clinical development
Paginering:
Jaargang 3 (2016) nr. C pagina's 1 p.
Jaar:
2016
Inhoud:
Uitgever:
Official journal of the American Society of Gene & Cell Therapy