Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy
Titel:
Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy
Auteur:
Armbruster, Nicole Lattanzi, Annalisa Jeavons, Matthieu Van Wittenberghe, Laetitia Gjata, Bernard Marais, Thibaut Martin, Samia Vignaud, Alban Voit, Thomas Mavilio, Fulvio Barkats, Martine Buj-Bello, Ana
Verschenen in:
Molecular therapy. Methods & clinical development
Paginering:
Jaargang 3 (2016) nr. C pagina's 1 p.
Jaar:
2016
Inhoud:
Uitgever:
Official journal of the American Society of Gene & Cell Therapy