| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear
|
Ivanchenko, Maryna V.
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|
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21 |
C |
p. 382-398
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artikel
|
| 2 |
Acerola exosome-like nanovesicles to systemically deliver nucleic acid medicine via oral administration
|
Umezu, Tomohiro
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|
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21 |
C |
p. 199-208
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artikel
|
| 3 |
Adeno-associated virus serotype 9 antibodies in patients screened for treatment with onasemnogene abeparvovec
|
Day, John W.
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21 |
C |
p. 76-82
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artikel
|
| 4 |
Adipose-derived stem cells protect motor neurons and reduce glial activation in both in vitro and in vivo models of ALS
|
Ciervo, Yuri
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|
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21 |
C |
p. 413-433
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artikel
|
| 5 |
Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss
|
Bankoti, Kamakshi
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|
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21 |
C |
p. 209-236
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artikel
|
| 6 |
A hierarchical and collaborative BRD4/CEBPD partnership governs vascular smooth muscle cell inflammation
|
Wang, Qingwei
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|
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21 |
C |
p. 54-66
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artikel
|
| 7 |
Alginate hydrogel polymers enable efficient delivery of a vascular-targeted AAV vector into aortic tissue
|
Remes, Anca
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|
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21 |
C |
p. 83-93
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artikel
|
| 8 |
A Library-Based Screening Strategy for the Identification of DARPins as Ligands for Receptor-Targeted AAV and Lentiviral Vectors
|
Hartmann, Jessica
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|
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21 |
C |
p. 728
|
artikel
|
| 9 |
Analytical band centrifugation for the separation and quantification of empty and full AAV particles
|
Khasa, Harshit
|
|
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21 |
C |
p. 585-591
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artikel
|
| 10 |
Anion-exchange HPLC assay for separation and quantification of empty and full capsids in multiple adeno-associated virus serotypes
|
Khatwani, Santoshkumar L.
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|
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21 |
C |
p. 548-558
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artikel
|
| 11 |
Anti-CD19 CARs displayed at the surface of lentiviral vector particles promote transduction of target-expressing cells
|
Cordes, Nicole
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|
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21 |
C |
p. 42-53
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artikel
|
| 12 |
A pro-inflammatory mediator USP11 enhances the stability of p53 and inhibits KLF2 in intracerebral hemorrhage
|
Zhang, Xiuqing
|
|
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21 |
C |
p. 681-692
|
artikel
|
| 13 |
Autologous antigen-presenting cells efficiently expand piggyBac transposon CAR-T cells with predominant memory phenotype
|
Nakamura, Kayoko
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|
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21 |
C |
p. 315-324
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artikel
|
| 14 |
Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease
|
Uchida, Naoya
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|
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21 |
C |
p. 121-132
|
artikel
|
| 15 |
Cell-penetrating peptides enhance the transduction of adeno-associated virus serotype 9 in the central nervous system
|
Meng, Yuan
|
|
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21 |
C |
p. 28-41
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artikel
|
| 16 |
Central nervous system-targeted adeno-associated virus gene therapy in methylmalonic acidemia
|
May, Francis J.
|
|
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21 |
C |
p. 765-776
|
artikel
|
| 17 |
Comparing the efficacy of γ- and electron-irradiation of PBMCs to promote secretion of paracrine, regenerative factors
|
Laggner, Maria
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|
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21 |
C |
p. 14-27
|
artikel
|
| 18 |
CRISPAltRations: A validated cloud-based approach for interrogation of double-strand break repair mediated by CRISPR genome editing
|
Kurgan, Gavin
|
|
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21 |
C |
p. 478-491
|
artikel
|
| 19 |
Development of a scalable and robust AEX method for enriched rAAV preparations in genome-containing VCs of serotypes 5, 6, 8, and 9
|
Joshi, Pranav R.H.
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|
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21 |
C |
p. 341-356
|
artikel
|
| 20 |
Discovery of bone morphogenetic protein 7-derived peptide sequences that attenuate the human osteoarthritic chondrocyte phenotype
|
Caron, Marjolein M.J.
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|
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21 |
C |
p. 247-261
|
artikel
|
| 21 |
Discovery of key genes as novel biomarkers specifically associated with HPV-negative cervical cancer
|
Liu, Yi
|
|
|
21 |
C |
p. 492-506
|
artikel
|
| 22 |
Effect of epitope variant co-delivery on the depth of CD8 T cell responses induced by HIV-1 conserved mosaic vaccines
|
Wee, Edmund G.
|
|
|
21 |
C |
p. 741-753
|
artikel
|
| 23 |
Efficient CRISPR-Cas9-based genome editing of β-globin gene on erythroid cells from homozygous β039-thalassemia patients
|
Cosenza, Lucia Carmela
|
|
|
21 |
C |
p. 507-523
|
artikel
|
| 24 |
Efficient lentiviral transduction method to gene modify cord blood CD8+ T cells for cancer therapy applications
|
Lo Presti, Vania
|
|
|
21 |
C |
p. 357-368
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artikel
|
| 25 |
Engineering mesenchymal stromal cells with neutralizing and anti-inflammatory capability against SARS-CoV-2 infection
|
Zhang, Xiaoqing
|
|
|
21 |
C |
p. 754-764
|
artikel
|
| 26 |
Functional recovery of a novel knockin mouse model of dysferlinopathy by readthrough of nonsense mutation
|
Seo, Kyowon
|
|
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21 |
C |
p. 702-709
|
artikel
|
| 27 |
Generation of macrophages with altered viral sensitivity from genome-edited rhesus macaque iPSCs to model human disease
|
Iwamoto, Yoshihiro
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|
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21 |
C |
p. 262-273
|
artikel
|
| 28 |
Genetically blocking HPD via CRISPR-Cas9 protects against lethal liver injury in a pig model of tyrosinemia type I
|
Gu, Peng
|
|
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21 |
C |
p. 530-547
|
artikel
|
| 29 |
Global regulatory progress in delivering on the promise of gene therapies for unmet medical needs
|
Drago, Daniela
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|
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21 |
C |
p. 524-529
|
artikel
|
| 30 |
HIV-based lentiviral vectors: Origin and sequence differences
|
Johnson, Nathan M.
|
|
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21 |
C |
p. 451-465
|
artikel
|
| 31 |
Impact of intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II
|
Seo, Joo-Hyun
|
|
|
21 |
C |
p. 67-75
|
artikel
|
| 32 |
Improved safety of induced pluripotent stem cell-derived antigen-presenting cell-based cancer immunotherapy
|
Mashima, Hiroaki
|
|
|
21 |
C |
p. 171-179
|
artikel
|
| 33 |
Improvement of HSV-1 based amplicon vectors for a safe and long-lasting gene therapy in non-replicating cells
|
Soukupová, Marie
|
|
|
21 |
C |
p. 399-412
|
artikel
|
| 34 |
Increased CFTR expression and function from an optimized lentiviral vector for cystic fibrosis gene therapy
|
Marquez Loza, Laura I.
|
|
|
21 |
C |
p. 94-106
|
artikel
|
| 35 |
Induced dendritic cells co-expressing GM-CSF/IFN-α/tWT1 priming T and B cells and automated manufacturing to boost GvL
|
Bialek-Waldmann, Julia K.
|
|
|
21 |
C |
p. 621-641
|
artikel
|
| 36 |
In vitro characterization of engineered red blood cells as viral traps against HIV-1 and SARS-CoV-2
|
Hoffmann, Magnus A.G.
|
|
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21 |
C |
p. 161-170
|
artikel
|
| 37 |
In vivo targeting of lentiviral vectors pseudotyped with the Tupaia paramyxovirus H glycoprotein bearing a cell-specific ligand
|
Argaw, Takele
|
|
|
21 |
C |
p. 670-680
|
artikel
|
| 38 |
Machine learning prediction of methionine and tryptophan photooxidation susceptibility
|
Delmar, Jared A.
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|
|
21 |
C |
p. 466-477
|
artikel
|
| 39 |
Manufacturing NKG2D CAR-T cells with piggyBac transposon vectors and K562 artificial antigen-presenting cells
|
Tay, Johan C.K.
|
|
|
21 |
C |
p. 107-120
|
artikel
|
| 40 |
Mechanistic model for production of recombinant adeno-associated virus via triple transfection of HEK293 cells
|
Nguyen, Tam N.T.
|
|
|
21 |
C |
p. 642-655
|
artikel
|
| 41 |
Micro-laminin gene therapy can function as an inhibitor of muscle disease in the dyW mouse model of MDC1A
|
Packer, Davin
|
|
|
21 |
C |
p. 274-287
|
artikel
|
| 42 |
NaCl and KCl mediate log increase in AAV vector particles and infectious titers in a specific/timely manner with the HSV platform
|
Yu, Chenghui
|
|
|
21 |
C |
p. 1-13
|
artikel
|
| 43 |
Non-genotoxic conditioning facilitates hematopoietic stem cell gene therapy for hemophilia A using bioengineered factor VIII
|
Russell, Athena L.
|
|
|
21 |
C |
p. 710-727
|
artikel
|
| 44 |
Potent programmable antiviral against dengue virus in primary human cells by Cas13b RNP with short spacer and delivery by VLP
|
Singsuksawat, Ekapot
|
|
|
21 |
C |
p. 729-740
|
artikel
|
| 45 |
Pre-clinical dose-escalation studies establish a therapeutic range for U7snRNA-mediated DMD exon 2 skipping
|
Simmons, Tabatha R.
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|
|
21 |
C |
p. 325-340
|
artikel
|
| 46 |
Promoter usage regulating the surface density of CAR molecules may modulate the kinetics of CAR-T cells in vivo
|
Ho, Jin-Yuan
|
|
|
21 |
C |
p. 237-246
|
artikel
|
| 47 |
Reprogramming the anti-tumor immune response via CRISPR genetic and epigenetic editing
|
Alves, Eric
|
|
|
21 |
C |
p. 592-606
|
artikel
|
| 48 |
Robust hepatitis B vaccine-reactive T cell responses in failed humoral immunity
|
Awad, Gounwa
|
|
|
21 |
C |
p. 288-298
|
artikel
|
| 49 |
Robust induction of TRMs by combinatorial nanoshells confers cross-strain sterilizing immunity against lethal influenza viruses
|
Lin, Pin-Hung
|
|
|
21 |
C |
p. 299-314
|
artikel
|
| 50 |
Single amino acid insertion allows functional transduction of murine hepatocytes with human liver tropic AAV capsids
|
Cabanes-Creus, Marti
|
|
|
21 |
C |
p. 607-620
|
artikel
|
| 51 |
Synapsin-caveolin-1 gene therapy preserves neuronal and synaptic morphology and prevents neurodegeneration in a mouse model of AD
|
Wang, Shanshan
|
|
|
21 |
C |
p. 434-450
|
artikel
|
| 52 |
Targeted knockdown of the adenosine A2A receptor by lipid NPs rescues the chemotaxis of head and neck cancer memory T cells
|
Newton, Hannah S.
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|
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21 |
C |
p. 133-143
|
artikel
|
| 53 |
Targeting the Apoa1 locus for liver-directed gene therapy
|
De Giorgi, Marco
|
|
|
21 |
C |
p. 656-669
|
artikel
|
| 54 |
Testing the efficacy of a human full-length OPG-Fc analog in a severe model of cardiotoxin-induced skeletal muscle injury and repair
|
Bouredji, Zineb
|
|
|
21 |
C |
p. 559-573
|
artikel
|
| 55 |
The impact of lentiviral vector genome size and producer cell genomic to gag-pol mRNA ratios on packaging efficiency and titre
|
Sweeney, Nathan P.
|
|
|
21 |
C |
p. 574-584
|
artikel
|
| 56 |
Transplantation of miPSC/mESC-derived retinal ganglion cells into healthy and glaucomatous retinas
|
Oswald, Julia
|
|
|
21 |
C |
p. 180-198
|
artikel
|
| 57 |
3’ UTR-truncated HMGA2 overexpression induces non-malignant in vivo expansion of hematopoietic stem cells in non-human primates
|
Bonner, Melissa A.
|
|
|
21 |
C |
p. 693-701
|
artikel
|
| 58 |
VEGFR-1/Flt-1 inhibition increases angiogenesis and improves muscle function in a mouse model of Duchenne muscular dystrophy
|
Bosco, Jennifer
|
|
|
21 |
C |
p. 369-381
|
artikel
|
| 59 |
Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice
|
Hamm, Shelby E.
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21 |
C |
p. 144-160
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artikel
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