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Genetically blocking HPD via CRISPR-Cas9 protects against lethal liver injury in a pig model of tyrosinemia type I |
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Titel: |
Genetically blocking HPD via CRISPR-Cas9 protects against lethal liver injury in a pig model of tyrosinemia type I |
Auteur: |
Gu, Peng Yang, Qin Chen, Bangzhu Bie, Ya-nan Liu, Wen Tian, Yuguang Luo, Hongquan Xu, Tao Liang, Chunjin Ye, Xing Liu, Yan Tang, Xiangwu Gu, Weiwang |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 21 () nr. C pagina's 530-547 |
Jaar: |
2021 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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