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59 results found

no	title	author	magazine	year	volume	issue	page(s)	type
1	AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear	Ivanchenko, Maryna V.			21	C	p. 382-398	article
2	Acerola exosome-like nanovesicles to systemically deliver nucleic acid medicine via oral administration	Umezu, Tomohiro			21	C	p. 199-208	article
3	Adeno-associated virus serotype 9 antibodies in patients screened for treatment with onasemnogene abeparvovec	Day, John W.			21	C	p. 76-82	article
4	Adipose-derived stem cells protect motor neurons and reduce glial activation in both in vitro and in vivo models of ALS	Ciervo, Yuri			21	C	p. 413-433	article
5	Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss	Bankoti, Kamakshi			21	C	p. 209-236	article
6	A hierarchical and collaborative BRD4/CEBPD partnership governs vascular smooth muscle cell inflammation	Wang, Qingwei			21	C	p. 54-66	article
7	Alginate hydrogel polymers enable efficient delivery of a vascular-targeted AAV vector into aortic tissue	Remes, Anca			21	C	p. 83-93	article
8	A Library-Based Screening Strategy for the Identification of DARPins as Ligands for Receptor-Targeted AAV and Lentiviral Vectors	Hartmann, Jessica			21	C	p. 728	article
9	Analytical band centrifugation for the separation and quantification of empty and full AAV particles	Khasa, Harshit			21	C	p. 585-591	article
10	Anion-exchange HPLC assay for separation and quantification of empty and full capsids in multiple adeno-associated virus serotypes	Khatwani, Santoshkumar L.			21	C	p. 548-558	article
11	Anti-CD19 CARs displayed at the surface of lentiviral vector particles promote transduction of target-expressing cells	Cordes, Nicole			21	C	p. 42-53	article
12	A pro-inflammatory mediator USP11 enhances the stability of p53 and inhibits KLF2 in intracerebral hemorrhage	Zhang, Xiuqing			21	C	p. 681-692	article
13	Autologous antigen-presenting cells efficiently expand piggyBac transposon CAR-T cells with predominant memory phenotype	Nakamura, Kayoko			21	C	p. 315-324	article
14	Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease	Uchida, Naoya			21	C	p. 121-132	article
15	Cell-penetrating peptides enhance the transduction of adeno-associated virus serotype 9 in the central nervous system	Meng, Yuan			21	C	p. 28-41	article
16	Central nervous system-targeted adeno-associated virus gene therapy in methylmalonic acidemia	May, Francis J.			21	C	p. 765-776	article
17	Comparing the efficacy of γ- and electron-irradiation of PBMCs to promote secretion of paracrine, regenerative factors	Laggner, Maria			21	C	p. 14-27	article
18	CRISPAltRations: A validated cloud-based approach for interrogation of double-strand break repair mediated by CRISPR genome editing	Kurgan, Gavin			21	C	p. 478-491	article
19	Development of a scalable and robust AEX method for enriched rAAV preparations in genome-containing VCs of serotypes 5, 6, 8, and 9	Joshi, Pranav R.H.			21	C	p. 341-356	article
20	Discovery of bone morphogenetic protein 7-derived peptide sequences that attenuate the human osteoarthritic chondrocyte phenotype	Caron, Marjolein M.J.			21	C	p. 247-261	article
21	Discovery of key genes as novel biomarkers specifically associated with HPV-negative cervical cancer	Liu, Yi			21	C	p. 492-506	article
22	Effect of epitope variant co-delivery on the depth of CD8 T cell responses induced by HIV-1 conserved mosaic vaccines	Wee, Edmund G.			21	C	p. 741-753	article
23	Efficient CRISPR-Cas9-based genome editing of β-globin gene on erythroid cells from homozygous β039-thalassemia patients	Cosenza, Lucia Carmela			21	C	p. 507-523	article
24	Efficient lentiviral transduction method to gene modify cord blood CD8+ T cells for cancer therapy applications	Lo Presti, Vania			21	C	p. 357-368	article
25	Engineering mesenchymal stromal cells with neutralizing and anti-inflammatory capability against SARS-CoV-2 infection	Zhang, Xiaoqing			21	C	p. 754-764	article
26	Functional recovery of a novel knockin mouse model of dysferlinopathy by readthrough of nonsense mutation	Seo, Kyowon			21	C	p. 702-709	article
27	Generation of macrophages with altered viral sensitivity from genome-edited rhesus macaque iPSCs to model human disease	Iwamoto, Yoshihiro			21	C	p. 262-273	article
28	Genetically blocking HPD via CRISPR-Cas9 protects against lethal liver injury in a pig model of tyrosinemia type I	Gu, Peng			21	C	p. 530-547	article
29	Global regulatory progress in delivering on the promise of gene therapies for unmet medical needs	Drago, Daniela			21	C	p. 524-529	article
30	HIV-based lentiviral vectors: Origin and sequence differences	Johnson, Nathan M.			21	C	p. 451-465	article
31	Impact of intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II	Seo, Joo-Hyun			21	C	p. 67-75	article
32	Improved safety of induced pluripotent stem cell-derived antigen-presenting cell-based cancer immunotherapy	Mashima, Hiroaki			21	C	p. 171-179	article
33	Improvement of HSV-1 based amplicon vectors for a safe and long-lasting gene therapy in non-replicating cells	Soukupová, Marie			21	C	p. 399-412	article
34	Increased CFTR expression and function from an optimized lentiviral vector for cystic fibrosis gene therapy	Marquez Loza, Laura I.			21	C	p. 94-106	article
35	Induced dendritic cells co-expressing GM-CSF/IFN-α/tWT1 priming T and B cells and automated manufacturing to boost GvL	Bialek-Waldmann, Julia K.			21	C	p. 621-641	article
36	In vitro characterization of engineered red blood cells as viral traps against HIV-1 and SARS-CoV-2	Hoffmann, Magnus A.G.			21	C	p. 161-170	article
37	In vivo targeting of lentiviral vectors pseudotyped with the Tupaia paramyxovirus H glycoprotein bearing a cell-specific ligand	Argaw, Takele			21	C	p. 670-680	article
38	Machine learning prediction of methionine and tryptophan photooxidation susceptibility	Delmar, Jared A.			21	C	p. 466-477	article
39	Manufacturing NKG2D CAR-T cells with piggyBac transposon vectors and K562 artificial antigen-presenting cells	Tay, Johan C.K.			21	C	p. 107-120	article
40	Mechanistic model for production of recombinant adeno-associated virus via triple transfection of HEK293 cells	Nguyen, Tam N.T.			21	C	p. 642-655	article
41	Micro-laminin gene therapy can function as an inhibitor of muscle disease in the dyW mouse model of MDC1A	Packer, Davin			21	C	p. 274-287	article
42	NaCl and KCl mediate log increase in AAV vector particles and infectious titers in a specific/timely manner with the HSV platform	Yu, Chenghui			21	C	p. 1-13	article
43	Non-genotoxic conditioning facilitates hematopoietic stem cell gene therapy for hemophilia A using bioengineered factor VIII	Russell, Athena L.			21	C	p. 710-727	article
44	Potent programmable antiviral against dengue virus in primary human cells by Cas13b RNP with short spacer and delivery by VLP	Singsuksawat, Ekapot			21	C	p. 729-740	article
45	Pre-clinical dose-escalation studies establish a therapeutic range for U7snRNA-mediated DMD exon 2 skipping	Simmons, Tabatha R.			21	C	p. 325-340	article
46	Promoter usage regulating the surface density of CAR molecules may modulate the kinetics of CAR-T cells in vivo	Ho, Jin-Yuan			21	C	p. 237-246	article
47	Reprogramming the anti-tumor immune response via CRISPR genetic and epigenetic editing	Alves, Eric			21	C	p. 592-606	article
48	Robust hepatitis B vaccine-reactive T cell responses in failed humoral immunity	Awad, Gounwa			21	C	p. 288-298	article
49	Robust induction of TRMs by combinatorial nanoshells confers cross-strain sterilizing immunity against lethal influenza viruses	Lin, Pin-Hung			21	C	p. 299-314	article
50	Single amino acid insertion allows functional transduction of murine hepatocytes with human liver tropic AAV capsids	Cabanes-Creus, Marti			21	C	p. 607-620	article
51	Synapsin-caveolin-1 gene therapy preserves neuronal and synaptic morphology and prevents neurodegeneration in a mouse model of AD	Wang, Shanshan			21	C	p. 434-450	article
52	Targeted knockdown of the adenosine A2A receptor by lipid NPs rescues the chemotaxis of head and neck cancer memory T cells	Newton, Hannah S.			21	C	p. 133-143	article
53	Targeting the Apoa1 locus for liver-directed gene therapy	De Giorgi, Marco			21	C	p. 656-669	article
54	Testing the efficacy of a human full-length OPG-Fc analog in a severe model of cardiotoxin-induced skeletal muscle injury and repair	Bouredji, Zineb			21	C	p. 559-573	article
55	The impact of lentiviral vector genome size and producer cell genomic to gag-pol mRNA ratios on packaging efficiency and titre	Sweeney, Nathan P.			21	C	p. 574-584	article
56	Transplantation of miPSC/mESC-derived retinal ganglion cells into healthy and glaucomatous retinas	Oswald, Julia			21	C	p. 180-198	article
57	3’ UTR-truncated HMGA2 overexpression induces non-malignant in vivo expansion of hematopoietic stem cells in non-human primates	Bonner, Melissa A.			21	C	p. 693-701	article
58	VEGFR-1/Flt-1 inhibition increases angiogenesis and improves muscle function in a mouse model of Duchenne muscular dystrophy	Bosco, Jennifer			21	C	p. 369-381	article
59	Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice	Hamm, Shelby E.			21	C	p. 144-160	article

59 results found

Koninklijke Bibliotheek - National Library of the Netherlands