| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice
|
Colella, Pasqualina
|
|
2019
|
12 |
C |
p. 85-101
|
artikel
|
| 2 |
A Self-Deleting AAV-CRISPR System for In Vivo Genome Editing
|
Li, Ang
|
|
2019
|
12 |
C |
p. 111-122
|
artikel
|
| 3 |
Capsid Modifications for Targeting and Improving the Efficacy of AAV Vectors
|
Büning, Hildegard
|
|
2019
|
12 |
C |
p. 248-265
|
artikel
|
| 4 |
Codon-Optimization of Wild-Type Adeno-Associated Virus Capsid Sequences Enhances DNA Family Shuffling while Conserving Functionality
|
Cabanes-Creus, Marti
|
|
2019
|
12 |
C |
p. 71-84
|
artikel
|
| 5 |
Development of a Novel Anti-CD19 Chimeric Antigen Receptor: A Paradigm for an Affordable CAR T Cell Production at Academic Institutions
|
Castella, Maria
|
|
2019
|
12 |
C |
p. 134-144
|
artikel
|
| 6 |
Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model
|
Woodley, Evan
|
|
2019
|
12 |
C |
p. 47-57
|
artikel
|
| 7 |
Efficient Induction of T Cells against Conserved HIV-1 Regions by Mosaic Vaccines Delivered as Self-Amplifying mRNA
|
Moyo, Nathifa
|
|
2019
|
12 |
C |
p. 32-46
|
artikel
|
| 8 |
Engineering and Design of Chimeric Antigen Receptors
|
Guedan, Sonia
|
|
2019
|
12 |
C |
p. 145-156
|
artikel
|
| 9 |
Engineering Globin Gene Expression
|
Davis, Rachael
|
|
2019
|
12 |
C |
p. 102-110
|
artikel
|
| 10 |
Engineering Nanoparticles for Targeted Delivery of Nucleic Acid Therapeutics in Tumor
|
Xiao, Yao
|
|
2019
|
12 |
C |
p. 1-18
|
artikel
|
| 11 |
Intravenous Injection of an AAV-PHP.B Vector Encoding Human Acid α-Glucosidase Rescues Both Muscle and CNS Defects in Murine Pompe Disease
|
Lim, Jeong-A
|
|
2019
|
12 |
C |
p. 233-245
|
artikel
|
| 12 |
Novel Chimeric Gene Therapy Vectors Based on Adeno-Associated Virus and Four Different Mammalian Bocaviruses
|
Fakhiri, Julia
|
|
2019
|
12 |
C |
p. 202-222
|
artikel
|
| 13 |
Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome
|
Collaud, Fanny
|
|
2019
|
12 |
C |
p. 157-174
|
artikel
|
| 14 |
Preproinsulin Designer Antigens Excluded from Endoplasmic Reticulum Suppressed Diabetes Development in NOD Mice by DNA Vaccination
|
Stifter, Katja
|
|
2019
|
12 |
C |
p. 123-133
|
artikel
|
| 15 |
Protein-Engineered Coagulation Factors for Hemophilia Gene Therapy
|
Samelson-Jones, Benjamin J.
|
|
2019
|
12 |
C |
p. 184-201
|
artikel
|
| 16 |
Rational Design of Gene Therapy Vectors
|
Pan, Dao
|
|
2019
|
12 |
C |
p. 246-247
|
artikel
|
| 17 |
Shifting Retroviral Vector Integrations Away from Transcriptional Start Sites via DNA-Binding Protein Domain Insertion into Integrase
|
Nam, Jung-soo
|
|
2019
|
12 |
C |
p. 58-70
|
artikel
|
| 18 |
Surface-Engineered Lentiviral Vectors for Selective Gene Transfer into Subtypes of Lymphocytes
|
Frank, Annika M.
|
|
2019
|
12 |
C |
p. 19-31
|
artikel
|
| 19 |
TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin Induction
|
Lux, Christopher T.
|
|
2019
|
12 |
C |
p. 175-183
|
artikel
|
| 20 |
Transcriptional Targeting and MicroRNA Regulation of Lentiviral Vectors
|
Merlin, Simone
|
|
2019
|
12 |
C |
p. 223-232
|
artikel
|
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