TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin Induction
Titel:
TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin Induction
Auteur:
Lux, Christopher T. Pattabhi, Sowmya Berger, Mason Nourigat, Cynthia Flowers, David A. Negre, Olivier Humbert, Olivier Yang, Julia G. Lee, Calvin Jacoby, Kyle Bernstein, Irwin Kiem, Hans-Peter Scharenberg, Andrew Rawlings, David J.