AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice
Titel:
AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice
Auteur:
Colella, Pasqualina Sellier, Pauline Costa Verdera, Helena Puzzo, Francesco van Wittenberghe, Laetitia Guerchet, Nicolas Daniele, Nathalie Gjata, Bernard Marmier, Solenne Charles, Severine Simon Sola, Marcelo Ragone, Isabella Leborgne, Christian Collaud, Fanny Mingozzi, Federico