| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A combination of systemic mannitol and mannitol modified polyester nanoparticles for caveolae-mediated gene delivery to the brain
|
Gilbert, Betsy Reshma
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36 |
1 |
p.
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artikel
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| 2 |
Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group
|
Cavazza, Alessia
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36 |
1 |
p.
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artikel
|
| 3 |
Albumin-conjugation enables improved tumor targeting of aptamers via SPECT imaging
|
Yang, Shaowen
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36 |
1 |
p.
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artikel
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| 4 |
A new program for SELEX sorting and visualization of aptamers
|
Rossi, John J.
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36 |
1 |
p.
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artikel
|
| 5 |
An mRNA vaccine induces antimycobacterial immunity by activating DNA damage repair and autophagy
|
Chen, Dan
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36 |
1 |
p.
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artikel
|
| 6 |
Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells
|
Anwar, Saeed
|
|
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36 |
1 |
p.
|
artikel
|
| 7 |
Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells
|
Suzuki, Naoki
|
|
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36 |
1 |
p.
|
artikel
|
| 8 |
A sort and sequence approach to dissect heterogeneity of response to a self-amplifying RNA vector in a novel human muscle cell line
|
Barton, Rachel D.
|
|
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36 |
1 |
p.
|
artikel
|
| 9 |
Axl deficiency promotes preeclampsia and vascular malformations in mice
|
Zhou, Chan
|
|
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36 |
1 |
p.
|
artikel
|
| 10 |
CleanCap M6 inhibits decapping of exogenously delivered IVT mRNA
|
Mandell, Zachary F.
|
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36 |
1 |
p.
|
artikel
|
| 11 |
Clinical trial to compare safety and tolerability between intravenous infusion and bolus intravenous injection of ApTOLL in healthy volunteers
|
Hernández-Jiménez, Macarena
|
|
|
36 |
1 |
p.
|
artikel
|
| 12 |
Computational approaches for identifying neuropeptides: A comprehensive review
|
Rahmani, Roya
|
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|
36 |
1 |
p.
|
artikel
|
| 13 |
COVID-19 mRNA vaccines are effective at stopping a nosy virus
|
Beloki, Uxue
|
|
|
36 |
1 |
p.
|
artikel
|
| 14 |
Decoding CKD-induced muscle atrophy through the critical role of lncRNA GAS5 and pyroptosis
|
Huang, Rong
|
|
|
36 |
1 |
p.
|
artikel
|
| 15 |
DeepAptamer: Advancing high-affinity aptamer discovery with a hybrid deep learning model
|
Yang, Xin
|
|
|
36 |
1 |
p.
|
artikel
|
| 16 |
Development and characterization of a miRNA-responsive circular RNA expression system with cell type specificity
|
Ma, Yu
|
|
|
36 |
1 |
p.
|
artikel
|
| 17 |
Development of a cell-penetrating peptide-based nanocomplex for long-term delivery of intact mitochondrial DNA into epithelial cells
|
Wilson, Kyrie
|
|
|
36 |
1 |
p.
|
artikel
|
| 18 |
Development of a rabbit model for adrenoleukodystrophy: A pilot study on gene therapy using rAAV9
|
Zhou, Xiaoya
|
|
|
36 |
1 |
p.
|
artikel
|
| 19 |
Development of novel nucleic acid therapy aimed at directly controlling liver fibrosis
|
Umezu, Tomohiro
|
|
|
36 |
1 |
p.
|
artikel
|
| 20 |
Development, opportunities, and challenges of siRNA nucleic acid drugs
|
Xiao, Bowen
|
|
|
36 |
1 |
p.
|
artikel
|
| 21 |
Discovery and characterization of stereodefined PMO-gapmers targeting tau
|
Kanatsu, Kunihiko
|
|
|
36 |
1 |
p.
|
artikel
|
| 22 |
Effective gene therapy for metachromatic leukodystrophy achieved with minimal lentiviral genomic integrations
|
Tricoli, Lucas
|
|
|
36 |
1 |
p.
|
artikel
|
| 23 |
Effect of chemical modification on the exon-skipping activity of heteroduplex oligonucleotides
|
Shimo, Takenori
|
|
|
36 |
1 |
p.
|
artikel
|
| 24 |
Engineering of SauriCas9 with enhanced specificity
|
Zhang, Xiaoqi
|
|
|
36 |
1 |
p.
|
artikel
|
| 25 |
Enhanced hammerhead ribozyme turnover rates: Reevaluating therapeutic space for small catalytic RNAs
|
Myers, Jason M.
|
|
|
36 |
1 |
p.
|
artikel
|
| 26 |
Enhanced HDR-mediated correction of heterozygous COL7A1 mutations for recessive dystrophic epidermolysis bullosa
|
Hunt, John M.T.
|
|
|
36 |
1 |
p.
|
artikel
|
| 27 |
Enhancing RNA editing efficiency and specificity with engineered ADAR2 guide RNAs
|
Ai, Xilei
|
|
|
36 |
1 |
p.
|
artikel
|
| 28 |
Extracellular viral microRNAs as biomarkers of virus infection in human cells
|
Chan, Cheryl
|
|
|
36 |
1 |
p.
|
artikel
|
| 29 |
Flow rate modulates focused ultrasound-mediated vascular delivery of microRNA
|
He, Stephanie
|
|
|
36 |
1 |
p.
|
artikel
|
| 30 |
FTO deficiency facilitates epithelia dysfunction in oral lichen planus
|
Fan, Yufeng
|
|
|
36 |
1 |
p.
|
artikel
|
| 31 |
Gal-3 activates Tyro3 to ameliorate ferroptosis of hippocampal neurons after traumatic brain injury
|
Zhang, Xiao
|
|
|
36 |
1 |
p.
|
artikel
|
| 32 |
Glutamine missense suppressor transfer RNAs inhibit polyglutamine aggregation
|
Tennakoon, Rasangi
|
|
|
36 |
1 |
p.
|
artikel
|
| 33 |
Harnessing defective interfering particles and lipid nanoparticles for effective delivery of an anti-dengue virus RNA therapy
|
Lin, Min-Hsuan
|
|
|
36 |
1 |
p.
|
artikel
|
| 34 |
Healing the heart, one variant at a time
|
Mohsin, Sadia
|
|
|
36 |
1 |
p.
|
artikel
|
| 35 |
High-accuracy crRNA array assembly strategy for multiplex CRISPR
|
Zhao, Xiangtong
|
|
|
36 |
1 |
p.
|
artikel
|
| 36 |
i-Motifs as regulatory switches: Mechanisms and implications for gene expression
|
Deep, Auroni
|
|
|
36 |
1 |
p.
|
artikel
|
| 37 |
Impact on efficacy of target reduction of two FDA-approved ASO drugs by intracellular glucose levels in in vitro cell models
|
Nguyen, Le Tra Giang
|
|
|
36 |
1 |
p.
|
artikel
|
| 38 |
Improving the potency prediction for chemically modified siRNAs through insights from molecular modeling of individual sequence positions
|
Kliuchnikov, Evgenii
|
|
|
36 |
1 |
p.
|
artikel
|
| 39 |
In vitro high-content screening reveals miR-429 as a protective molecule in photoreceptor degeneration
|
Petrogiannakis, Georgios
|
|
|
36 |
1 |
p.
|
artikel
|
| 40 |
In vivo efficacy and safety of systemically administered serinol nucleic acid-modified antisense oligonucleotides in mouse kidney
|
Tsuboi, Toshiki
|
|
|
36 |
1 |
p.
|
artikel
|
| 41 |
In vivo efficacy and safety of systemically administered serinol nucleic acid-modified antisense oligonucleotides in mouse kidney
|
Tsuboi, Toshiki
|
|
|
36 |
1 |
p.
|
artikel
|
| 42 |
In vivo production of engineered ACE2 decoy protects lungs from SARS-CoV-2 infection
|
Suzuki, Yuta
|
|
|
36 |
1 |
p.
|
artikel
|
| 43 |
lncRNA localization and feature interpretability analysis
|
Li, Jing
|
|
|
36 |
1 |
p.
|
artikel
|
| 44 |
Lockpicking FGFR1 with aptamer-based technology
|
Nonatelli, Francesca
|
|
|
36 |
1 |
p.
|
artikel
|
| 45 |
miR-125b differentially impacts mineralization in dexamethasone and calcium-treated human mesenchymal stem cells
|
Joris, Virginie
|
|
|
36 |
1 |
p.
|
artikel
|
| 46 |
miR-429 RNA therapy as generic strategy to protect against photoreceptor loss
|
Wijnholds, Jan
|
|
|
36 |
1 |
p.
|
artikel
|
| 47 |
Modeling and correction of protein conformational disease in iPSC-derived neurons through personalized base editing
|
Konishi, Colin T.
|
|
|
36 |
1 |
p.
|
artikel
|
| 48 |
mRNA-1273 is placenta-permeable and immunogenic in the fetus
|
Chen, Jeng-Chang
|
|
|
36 |
1 |
p.
|
artikel
|
| 49 |
MSCs act as biopatches for blood-retinal barrier preservation to enhance functional recovery after retinal I/R
|
Wei, Xiaoyue
|
|
|
36 |
1 |
p.
|
artikel
|
| 50 |
Multi-omic insights into molecular mechanism and therapeutic targets in spinocerebellar ataxia type 7
|
Ahn, Soo Hyun
|
|
|
36 |
1 |
p.
|
artikel
|
| 51 |
Multi-omics and machine learning-driven CD8+ T cell heterogeneity score for head and neck squamous cell carcinoma
|
He, Di
|
|
|
36 |
1 |
p.
|
artikel
|
| 52 |
Non-invasive detection of allele-specific CRISPR-SaCas9-KKH disruption of TOR1A DYT1 allele in a xenograft mouse model
|
Maalouf, Katia E.
|
|
|
36 |
1 |
p.
|
artikel
|
| 53 |
Nucleic acid delivery for pathology treatment: RNA tissue delivery
|
Scalabrin, Silvia
|
|
|
36 |
1 |
p.
|
artikel
|
| 54 |
Nucleic acid therapeutics: Past, present, and future
|
Naeem, Sajid
|
|
|
36 |
1 |
p.
|
artikel
|
| 55 |
Overexpression of lncRNA EPB41L4A-AS1 Induces Metabolic Reprogramming in Trophoblast Cells and Placenta Tissue of Miscarriage
|
Zhu, Yuanchang
|
|
|
36 |
1 |
p.
|
artikel
|
| 56 |
Pan-cancer characterization of m6A-mediated regulation of T cell exhaustion dynamics and clinical relevancies in human cancers
|
Ji, Weiping
|
|
|
36 |
1 |
p.
|
artikel
|
| 57 |
Personalized allele-specific antisense oligonucleotides for GNAO1-neurodevelopmental disorder
|
Shomer, Inna
|
|
|
36 |
1 |
p.
|
artikel
|
| 58 |
piRNA/PIWI pathways and epigenetic crosstalk in human diseases: Molecular insights into HIV-1 infection and drugs of abuse
|
Chennakesavan, Karthick
|
|
|
36 |
1 |
p.
|
artikel
|
| 59 |
Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S
|
Smieszek, Sandra
|
|
|
36 |
1 |
p.
|
artikel
|
| 60 |
Precise template-free correction restores gene function in Tay-Sachs disease while reframing is ineffective
|
Hung, Joshua E.
|
|
|
36 |
1 |
p.
|
artikel
|
| 61 |
Ratio of miRNA-29 to miRNA-199 expression coordinates mesenchymal stem cell repair of bleomycin-induced pulmonary injury
|
Elliot, Sharon J.
|
|
|
36 |
1 |
p.
|
artikel
|
| 62 |
Redefining NSP12 activity in SARS-CoV-2 and its regulation by NSP8 and NSP7
|
Singh, Deepa
|
|
|
36 |
1 |
p.
|
artikel
|
| 63 |
Rescue of the disease-associated phenotype in CRISPR-corrected hiPSCs as a therapeutic approach for inherited retinal dystrophies
|
Siles, Laura
|
|
|
36 |
1 |
p.
|
artikel
|
| 64 |
Restoring hematopoietic stem and progenitor cell function in Fancc −/− mice by in situ delivery of RNA lipid nanoparticles
|
Banda, Omar
|
|
|
36 |
1 |
p.
|
artikel
|
| 65 |
Retraction Notice to: Promotion of tumor progression by exosome transmission of circular RNA circSKA3
|
Du, William W.
|
|
|
36 |
1 |
p.
|
artikel
|
| 66 |
RNA splicing variants of the novel long non-coding RNA, CyKILR, possess divergent biological functions in non-small cell lung cancer
|
Xie, Xiujie
|
|
|
36 |
1 |
p.
|
artikel
|
| 67 |
siRNA tackles cancer: Immune checkpoint inhibitors and siRNA combinations
|
Coles, Andrew H.
|
|
|
36 |
1 |
p.
|
artikel
|
| 68 |
SNA-modified antisense oligonucleotides: A new pathway for renal targeting?
|
Dumoulin, Bernhard
|
|
|
36 |
1 |
p.
|
artikel
|
| 69 |
Specific inhibition of fibroblast growth factor receptor 1 signaling by a DNA aptamer
|
Zlinska, Vladimira
|
|
|
36 |
1 |
p.
|
artikel
|
| 70 |
Splicing to orchestrate cell fate
|
Zhang, Xurui
|
|
|
36 |
1 |
p.
|
artikel
|
| 71 |
Targeted allele-specific FGFR2 knockdown via human recombinant ferritin nanoparticles for personalized treatment of Crouzon syndrome
|
Tiberio, Federica
|
|
|
36 |
1 |
p.
|
artikel
|
| 72 |
The applications of live attenuated influenza a virus with modified NS1 gene
|
Zhang, Hongbo
|
|
|
36 |
1 |
p.
|
artikel
|
| 73 |
The evolving landscape of NF gene therapy: Hurdles and opportunities
|
O’Donohue, Alexandra K.
|
|
|
36 |
1 |
p.
|
artikel
|
| 74 |
Therapeutic potential and microRNA regulating properties of phytochemicals in Alzheimer’s disease
|
Kumari, Ankita
|
|
|
36 |
1 |
p.
|
artikel
|
| 75 |
TMEM97 governs partial epithelial-mesenchymal transition of retinal pigment epithelial cells via the CTNND2-ADAM10 axis
|
Li, Jing
|
|
|
36 |
1 |
p.
|
artikel
|
| 76 |
Transcriptomic analysis of the immune response to in vivo gene electrotransfer in colorectal cancer
|
De Robertis, Mariangela
|
|
|
36 |
1 |
p.
|
artikel
|
| 77 |
U1 Adaptor Oligonucleotides Targeting BCL2 and GRM1 Suppress Growth of Human Melanoma Xenografts In Vivo
|
Goraczniak, Rafal
|
|
|
36 |
1 |
p.
|
artikel
|
| 78 |
Unleashing the TLR9-driven multilineage differentiation of myeloid leukemia cells in vivo
|
Piwocka, Katarzyna
|
|
|
36 |
1 |
p.
|
artikel
|
| 79 |
Unlocking RNA mysteries: Predicting subcellular localizations with AI
|
Le, Nguyen Quoc Khanh
|
|
|
36 |
1 |
p.
|
artikel
|
| 80 |
Unlocking the potential of allele-specific siRNA therapy: A novel approach for Crouzon syndrome
|
Di Rocco, Federico
|
|
|
36 |
1 |
p.
|
artikel
|
| 81 |
Unveiling sequence-agnostic mixed-chemical modification patterns for splice-switching oligonucleotides using the NATURA platform
|
Tabaglio, Tommaso
|
|
|
36 |
1 |
p.
|
artikel
|
| 82 |
uORF-targeting steric block antisense oligonucleotides do not reproducibly increase RNASEH1 expression
|
Ahlskog, Nina
|
|
|
36 |
1 |
p.
|
artikel
|
| 83 |
Use of an oversized AAV8 vector for CPS1 deficiency results in long-term survival and ammonia control
|
Diep, Taryn
|
|
|
36 |
1 |
p.
|
artikel
|
| 84 |
Use of polyadenosine tail mimetics to enhance mRNA expression from genes associated with haploinsufficiency disorders
|
Torkzaban, Bahareh
|
|
|
36 |
1 |
p.
|
artikel
|
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