Effective gene therapy for metachromatic leukodystrophy achieved with minimal lentiviral genomic integrations
Title:
Effective gene therapy for metachromatic leukodystrophy achieved with minimal lentiviral genomic integrations
Author:
Tricoli, Lucas Sase, Sunetra Hacker, Julia L. Pham, Vi Chappell, Maxwell Breda, Laura Hurwitz, Stephanie N. Tanaka, Naoto Castruccio Castracani, Carlo Guerra, Amaliris Hou, Zhongqi Schlotawa, Lars Radhakrishnan, Karthikeyan Hogenauer, Matthew Roche, Aoife Everett, John Bushman, Frederic Kurre, Peter Ahrens-Nicklas, Rebecca Adang, Laura A. Vanderver, Adeline L. Rivella, Stefano