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Modeling and correction of protein conformational disease in iPSC-derived neurons through personalized base editing |
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Titel: |
Modeling and correction of protein conformational disease in iPSC-derived neurons through personalized base editing |
Auteur: |
Konishi, Colin T. Mulaiese, Nancy Butola, Tanvi Zhang, Qinkun Kagan, Dana Yang, Qiaoyan Pressler, Mariel Dirvin, Brooke G. Devinsky, Orrin Basu, Jayeeta Long, Chengzu |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 36 () nr. 1 pagina's p. |
Jaar: |
2025 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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