| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A fleeting glimpse of functional benefit of the complete DMD gene in a large animal model of Duchenne muscular dystrophy
|
Hoffman, Eric P.
|
|
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33 |
C |
p. 938-940
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artikel
|
| 2 |
A neutralizable dimeric anti-thrombin aptamer with potent anticoagulant activity in mice
|
Nagano, Masanobu
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|
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33 |
C |
p. 762-772
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artikel
|
| 3 |
Angiotensin II mediates hypertensive cardiac fibrosis via an Erbb4-IR-dependent mechanism
|
Li, Jian-Chun
|
|
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33 |
C |
p. 180-190
|
artikel
|
| 4 |
An unbiased seed-based RNAi selection screen identifies small RNAs that inhibit androgen signaling and prostate cancer cell growth
|
Corbin, Joshua M.
|
|
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33 |
C |
p. 257-272
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artikel
|
| 5 |
Apolipoprotein E and viral infection: Risks and Mechanisms
|
Chen, Feng
|
|
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33 |
C |
p. 529-542
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artikel
|
| 6 |
Artificial intelligence enabled ChatGPT and large language models in drug target discovery, drug discovery, and development
|
Chakraborty, Chiranjib
|
|
|
33 |
C |
p. 866-868
|
artikel
|
| 7 |
Asymmetric trichotomous partitioning overcomes dataset limitations in building machine learning models for predicting siRNA efficacy
|
Monopoli, Kathryn R.
|
|
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33 |
C |
p. 93-109
|
artikel
|
| 8 |
Branchpoints as potential targets of exon-skipping therapies for genetic disorders
|
Ohara, Hiroaki
|
|
|
33 |
C |
p. 404-412
|
artikel
|
| 9 |
Bridging siRNA strands for better function
|
Rossi, John J.
|
|
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33 |
C |
p. 209
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artikel
|
| 10 |
Can artificial intelligence-strengthened ChatGPT or other large language models transform nucleic acid research?
|
Chatterjee, Srijan
|
|
|
33 |
C |
p. 205-207
|
artikel
|
| 11 |
Cancer kill code extension
|
Peter, Marcus E.
|
|
|
33 |
C |
p. 773
|
artikel
|
| 12 |
Cathepsin B-activatable cyclic antisense oligonucleotides for cell-specific target gene knockdown in vitro and in vivo
|
Wang, Zhongyu
|
|
|
33 |
C |
p. 548-558
|
artikel
|
| 13 |
Cell-type-specific alternative polyadenylation promotes oncogenic gene expression in non-small cell lung cancer progression
|
Huang, Kexin
|
|
|
33 |
C |
p. 816-831
|
artikel
|
| 14 |
Characterization of cooperative PS-oligo activation of human TLR9
|
Pollak, Adam J.
|
|
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33 |
C |
p. 832-844
|
artikel
|
| 15 |
Chloroquine and cytosolic galectins affect endosomal escape of antisense oligonucleotides after Stabilin-mediated endocytosis
|
Pandey, Ekta
|
|
|
33 |
C |
p. 430-443
|
artikel
|
| 16 |
Cis-Cardio: A comprehensive analysis platform for cardiovascular-relavant cis-regulation in human and mouse
|
Song, Chao
|
|
|
33 |
C |
p. 655-667
|
artikel
|
| 17 |
Combining independent protein and cellular SELEX with bioinformatic analysis may allow high affinity aptamer hit discovery
|
Ducrot, Coline
|
|
|
33 |
C |
p. 254-256
|
artikel
|
| 18 |
Combining nonsense mutation suppression therapy with nonsense-mediated decay inhibition in neurofibromatosis type 1
|
Osum, Sara H.
|
|
|
33 |
C |
p. 227-239
|
artikel
|
| 19 |
Construction of PANoptosis signature: Novel target discovery for prostate cancer immunotherapy
|
Yi, Xianyanling
|
|
|
33 |
C |
p. 376-390
|
artikel
|
| 20 |
Disease modeling and gene correction of LGMDR21 iPSCs elucidates the role of POGLUT1 in skeletal muscle maintenance, regeneration, and the satellite cell niche
|
Ortiz-Vitali, Jose L.
|
|
|
33 |
C |
p. 683-697
|
artikel
|
| 21 |
DNM2 levels normalization improves muscle phenotypes of a novel mouse model for moderate centronuclear myopathy
|
de Carvalho Neves, Juliana
|
|
|
33 |
C |
p. 321-334
|
artikel
|
| 22 |
Effects of Aptamer to U87-EGFRvIII Cells on the Proliferation, Radiosensitivity, and Radiotherapy of Glioblastoma Cells
|
Zhang, Xingmei
|
|
|
33 |
C |
p. 428-429
|
artikel
|
| 23 |
Efficient circular RNA engineering by end-to-end self-targeting and splicing reaction using Tetrahymena group I intron ribozyme
|
Lee, Kyung Hyun
|
|
|
33 |
C |
p. 587-598
|
artikel
|
| 24 |
Engineering B cells with customized therapeutic responses using a synthetic circuit
|
Page, Audrey
|
|
|
33 |
C |
p. 1-14
|
artikel
|
| 25 |
Epigenetic therapy: BBC1115, a novel BET inhibitor with broad antitumor activity
|
Cingaram, Pradeep Reddy
|
|
|
33 |
C |
p. 142-143
|
artikel
|
| 26 |
Estrogen-regulated miRs in bone enhance osteoblast differentiation and matrix mineralization
|
Emch, Michael J.
|
|
|
33 |
C |
p. 28-41
|
artikel
|
| 27 |
EV-mediated promotion of myogenic differentiation is dependent on dose, collection medium, and isolation method
|
Hanson, Britt
|
|
|
33 |
C |
p. 511-528
|
artikel
|
| 28 |
Expression of NORAD correlates with breast cancer aggressiveness and protects breast cancer cells from chemotherapy
|
Alves-Vale, Catarina
|
|
|
33 |
C |
p. 910-924
|
artikel
|
| 29 |
Fluorescent nanodiamonds as innovative delivery systems for MiR-34a replacement in breast cancer
|
Abate, Marianna
|
|
|
33 |
C |
p. 127-141
|
artikel
|
| 30 |
Forging the future of circRNA therapeutics: Unleashing synthetic potential and conquering challenges
|
Qi, Dan
|
|
|
33 |
C |
p. 42-43
|
artikel
|
| 31 |
Gymnotic uptake of AntimiRs alter microRNA-34a levels in 2D and 3D epithelial cell culture
|
Weidner, Julie
|
|
|
33 |
C |
p. 898-907
|
artikel
|
| 32 |
Harnessing the potential of lipid nanoparticles for the delivery of chemically modified siRNA to combat hepatic adenovirus infection
|
Shubhra, Quazi T.H.
|
|
|
33 |
C |
p. 44-46
|
artikel
|
| 33 |
Improved tropoelastin synthesis in the skin by codon optimization and nucleotide modification of tropoelastin-encoding synthetic mRNA
|
Golombek, Sonia
|
|
|
33 |
C |
p. 642-654
|
artikel
|
| 34 |
Inhibition of pro-inflammatory signaling in human primary macrophages by enhancing arginase-2 via target site blockers
|
Fitzsimons, Stephen
|
|
|
33 |
C |
p. 941-959
|
artikel
|
| 35 |
Insight into the regulatory mechanism of dynamic chromatin 3D interactions during cardiomyocyte differentiation in human
|
Liu, Hui
|
|
|
33 |
C |
p. 629-641
|
artikel
|
| 36 |
Integrated multiomics analysis and machine learning refine molecular subtypes and prognosis for muscle-invasive urothelial cancer
|
Chu, Guangdi
|
|
|
33 |
C |
p. 110-126
|
artikel
|
| 37 |
Intratumoral immunotherapy with mRNAs encoding chimeric protein constructs encompassing IL-12, CD137 agonists, and TGF-β antagonists
|
Cirella, Assunta
|
|
|
33 |
C |
p. 668-682
|
artikel
|
| 38 |
Intratumoral injection of IL-12-encoding mRNA targeted to CSF1R and PD-L1 exerts potent anti-tumor effects without substantial systemic exposure
|
Di Trani, Claudia Augusta
|
|
|
33 |
C |
p. 599-616
|
artikel
|
| 39 |
Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C
|
De Cristofaro, Raimondo
|
|
|
33 |
C |
p. 749
|
artikel
|
| 40 |
Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C
|
Martinez-Navajas, Gonzalo
|
|
|
33 |
C |
p. 75-92
|
artikel
|
| 41 |
Leverage of nuclease-deficient CasX for preventing pathological angiogenesis
|
Han, Haote
|
|
|
33 |
C |
p. 738-748
|
artikel
|
| 42 |
Lipid nanoparticle-targeted mRNA formulation as a treatment for ornithine-transcarbamylase deficiency model mice
|
Yamazaki, Kazuto
|
|
|
33 |
C |
p. 210-226
|
artikel
|
| 43 |
Long-term muscle-specific overexpression of DOK7 in mice using AAV9-tMCK-DOK7
|
Huang, Yu-Ting
|
|
|
33 |
C |
p. 617-628
|
artikel
|
| 44 |
MAVS is a double-edged sword
|
Huang, Christina
|
|
|
33 |
C |
p. 869-870
|
artikel
|
| 45 |
Mesenchymal stem cell engineering by ARCA analog-capped mRNA
|
Andrzejewska, Anna
|
|
|
33 |
C |
p. 454-468
|
artikel
|
| 46 |
MicroRNA-142a-3p regulates neurogenic skeletal muscle atrophy by targeting Mef2a
|
Gu, Xinyi
|
|
|
33 |
C |
p. 191-204
|
artikel
|
| 47 |
Mini-PE, a prime editor with compact Cas9 and truncated reverse transcriptase
|
Lan, Ting
|
|
|
33 |
C |
p. 890-897
|
artikel
|
| 48 |
Molnupiravir’s mechanism of action drives “error catastrophe” in SARS-CoV-2: A therapeutic strategy that leads to lethal mutagenesis of the virus
|
Chatterjee, Srijan
|
|
|
33 |
C |
p. 49-52
|
artikel
|
| 49 |
Nanoblades allow high-level genome editing in murine and human organoids
|
Tiroille, Victor
|
|
|
33 |
C |
p. 57-74
|
artikel
|
| 50 |
Non-viral in vivo cytidine base editing in hepatocytes using focused ultrasound targeted microbubbles
|
Anderson, Cynthia D.
|
|
|
33 |
C |
p. 733-737
|
artikel
|
| 51 |
Novel approaches to glaucomatous neurodegeneration, based on the integrated stress response
|
Chiarini, Luciana B.
|
|
|
33 |
C |
p. 845-847
|
artikel
|
| 52 |
Novel hybrid silicon-lipid nanoparticles deliver a siRNA to cure autosomal dominant osteopetrosis in mice. Implications for gene therapy in humans
|
Maurizi, Antonio
|
|
|
33 |
C |
p. 925-937
|
artikel
|
| 53 |
Nucleic acid amphiphiles: Synthesis, properties, and applications
|
Gubu, Amu
|
|
|
33 |
C |
p. 144-163
|
artikel
|
| 54 |
Overexpression of the mitochondrial anti-viral signaling protein, MAVS, in cancers is associated with cell survival and inflammation
|
Trishna, Sweta
|
|
|
33 |
C |
p. 713-732
|
artikel
|
| 55 |
Peptide nanostructures-based delivery of DNA nanomaterial therapeutics for regulating gene expression
|
Baral, Bineeth
|
|
|
33 |
C |
p. 493-510
|
artikel
|
| 56 |
Phenotypic features of dystrophin gene knockout pigs harboring a human artificial chromosome containing the entire dystrophin gene
|
Watanabe, Masahito
|
|
|
33 |
C |
p. 444-453
|
artikel
|
| 57 |
PINE-TREE enables efficient enrichment of prime-edited hPSCs
|
Jia, Mary S.
|
|
|
33 |
C |
p. 908-909
|
artikel
|
| 58 |
PINE-TREE enables highly efficient genetic modification of human cell lines
|
Frisch, Carlye
|
|
|
33 |
C |
p. 483-492
|
artikel
|
| 59 |
Potent dual block to HIV-1 infection using lentiviral vectors expressing fusion inhibitor peptide mC46- and Vif-resistant APOBEC3G
|
Delviks-Frankenberry, Krista A.
|
|
|
33 |
C |
p. 794-809
|
artikel
|
| 60 |
PPM1H is down-regulated by ATF6 and dephosphorylates p-RPS6KB1 to inhibit progression of hepatocellular carcinoma
|
Yang, Xiaoshuang
|
|
|
33 |
C |
p. 164-179
|
artikel
|
| 61 |
Protospacer modification improves base editing of a canonical splice site variant and recovery of CFTR function in human airway epithelial cells
|
Joynt, Anya T.
|
|
|
33 |
C |
p. 335-350
|
artikel
|
| 62 |
Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach
|
Centa, Jessica L.
|
|
|
33 |
C |
p. 15-27
|
artikel
|
| 63 |
Putting a stop to nonsense: Revisiting gene correction therapy for neurofibromatosis type 1
|
Gutmann, David H.
|
|
|
33 |
C |
p. 810-812
|
artikel
|
| 64 |
Quantum computing on nucleic acid research: Approaching towards next-generation computing
|
Chakraborty, Chiranjib
|
|
|
33 |
C |
p. 53-56
|
artikel
|
| 65 |
Restoration of functional PAX6 in aniridia patient iPSC-derived ocular tissue models using repurposed nonsense suppression drugs
|
Lima Cunha, Dulce
|
|
|
33 |
C |
p. 240-253
|
artikel
|
| 66 |
Retraction Notice to: lncRNA ILF3-AS1 promotes proliferation and metastasis of colorectal cancer cells by recruiting histone methylase EZH2
|
Hong, Sen
|
|
|
33 |
C |
p. 208
|
artikel
|
| 67 |
RGC-specific ATF4 and/or CHOP deletion rescues glaucomatous neurodegeneration and visual function
|
Fang, Fang
|
|
|
33 |
C |
p. 286-295
|
artikel
|
| 68 |
RNA nanoparticles for targeted therapies of triple-negative breast cancers
|
Danai, Leyla
|
|
|
33 |
C |
p. 885-886
|
artikel
|
| 69 |
Role of long non-coding RNAs in cancer: From subcellular localization to nanoparticle-mediated targeted regulation
|
Wei, Chunfang
|
|
|
33 |
C |
p. 774-793
|
artikel
|
| 70 |
Selection of a novel cell-internalizing RNA aptamer specific for CD22 antigen in B cell acute lymphoblastic leukemia
|
Ruiz-Ciancio, Dario
|
|
|
33 |
C |
p. 698-712
|
artikel
|
| 71 |
SINEUPs to boost translation
|
Oliviero, Salvatore
|
|
|
33 |
C |
p. 47-48
|
artikel
|
| 72 |
Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors
|
Gapinske, Michael
|
|
|
33 |
C |
p. 572-586
|
artikel
|
| 73 |
Targeting microRNA-145-mediated progressive phenotypes of early bladder cancer in a molecularly defined in vivo model
|
Heishima, Kazuki
|
|
|
33 |
C |
p. 960-982
|
artikel
|
| 74 |
Targeting oncogenic KRAS in non-small cell lung cancer with EGFR aptamer-conjugated multifunctional RNA nanoparticles
|
Yang, Linlin
|
|
|
33 |
C |
p. 559-571
|
artikel
|
| 75 |
Targeting triple-negative breast cancer cells with a β1-integrin binding aptamer
|
Pleiko, Karlis
|
|
|
33 |
C |
p. 871-884
|
artikel
|
| 76 |
The circular RNA Ataxia Telangiectasia Mutated regulates oxidative stress in smooth muscle cells in expanding abdominal aortic aneurysms
|
Fasolo, Francesca
|
|
|
33 |
C |
p. 848-865
|
artikel
|
| 77 |
The current landscape of long COVID clinical trials: NIH’s RECOVER to Stanford Medicine’s STOP-PASC initiative
|
Chakraborty, Chiranjib
|
|
|
33 |
C |
p. 887-889
|
artikel
|
| 78 |
The endosomal escape vehicle platform enhances delivery of oligonucleotides in preclinical models of neuromuscular disorders
|
Li, Xiang
|
|
|
33 |
C |
p. 273-285
|
artikel
|
| 79 |
Therapeutic inhibition of miR-155 attenuates liver fibrosis via STAT3 signaling
|
Bala, Shashi
|
|
|
33 |
C |
p. 413-427
|
artikel
|
| 80 |
Toward learning the rules that predict siRNA efficacy
|
Bofill-De Ros, Xavier
|
|
|
33 |
C |
p. 543-544
|
artikel
|
| 81 |
Trans-acting aptazyme for conditional gene knockdown in eukaryotic cells
|
Zhou, Shan
|
|
|
33 |
C |
p. 367-375
|
artikel
|
| 82 |
Treatment of autosomal dominant retinitis pigmentosa caused by RHO-P23H mutation with high-fidelity Cas13X in mice
|
Yan, Zixiang
|
|
|
33 |
C |
p. 750-761
|
artikel
|
| 83 |
Treatment of CHO cells with Taxol and reversine improves micronucleation and microcell-mediated chromosome transfer efficiency
|
Uno, Narumi
|
|
|
33 |
C |
p. 391-403
|
artikel
|
| 84 |
Tumor targeting and therapeutic assessments of RNA nanoparticles carrying α9-nAChR aptamer and anti-miR-21 in triple-negative breast cancers
|
Liao, You-Cheng
|
|
|
33 |
C |
p. 351-366
|
artikel
|
| 85 |
Two antisense RNAs—AFAP1-AS1 and MLK7-AS1—promote colorectal cancer progression by sponging miR-149-5p and miR-485-5p
|
Kim, Tae Won
|
|
|
33 |
C |
p. 305-320
|
artikel
|
| 86 |
Unveiling ATF6 and PPM1H signaling in hepatocellular carcinoma progression: From ER stress to tumor suppression
|
Iyer, Prajish
|
|
|
33 |
C |
p. 813-815
|
artikel
|
| 87 |
Unveiling the intricacies of gene delivery: Caveolae-mediated endocytosis induces efficient mRNA delivery in slow-dividing cells
|
den Roover, Sabine
|
|
|
33 |
C |
p. 545-547
|
artikel
|
| 88 |
VWA3A-derived ependyma promoter drives increased therapeutic protein secretion into the CSF
|
Carrell, Ellie M.
|
|
|
33 |
C |
p. 296-304
|
artikel
|
| 89 |
25 years of maturation: A systematic review of RNAi in the clinic
|
Corydon, Ida Juhl
|
|
|
33 |
C |
p. 469-482
|
artikel
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