Novel hybrid silicon-lipid nanoparticles deliver a siRNA to cure autosomal dominant osteopetrosis in mice. Implications for gene therapy in humans
Titel:
Novel hybrid silicon-lipid nanoparticles deliver a siRNA to cure autosomal dominant osteopetrosis in mice. Implications for gene therapy in humans
Auteur:
Maurizi, Antonio Patrizii, Piergiorgio Teti, Anna Sutera, Flavia Maria Baran-Rachwalska, Paulina Burns, Chris Nandi, Uttom Welsh, Michael Torabi-Pour, Nissim Dehsorkhi, Ashkan Saffie-Siebert, Suzanne