Protospacer modification improves base editing of a canonical splice site variant and recovery of CFTR function in human airway epithelial cells
Titel:
Protospacer modification improves base editing of a canonical splice site variant and recovery of CFTR function in human airway epithelial cells
Auteur:
Joynt, Anya T. Kavanagh, Erin W. Newby, Gregory A. Mitchell, Shakela Eastman, Alice C. Paul, Kathleen C. Bowling, Alyssa D. Osorio, Derek L. Merlo, Christian A. Patel, Shivani U. Raraigh, Karen S. Liu, David R. Sharma, Neeraj Cutting, Garry R.