Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Titel:
Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Auteur:
Gumusgoz, Emrah Guisso, Dikran R Kasiri, Sahba Wu, Jun Dear, Matthew Verhalen, Brandy Nitschke, Silvia Mitra, Sharmistha Nitschke, Felix Minassian, Berge A.
Verschenen in:
Neurotherapeutics
Paginering:
Jaargang 18 () nr. 2 pagina's 1414-1425
Jaar:
2021
Inhoud:
Uitgever:
The American Society for Experimental NeuroTherapeutics, Inc.