Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Title:
Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Author:
Gumusgoz, Emrah Guisso, Dikran R Kasiri, Sahba Wu, Jun Dear, Matthew Verhalen, Brandy Nitschke, Silvia Mitra, Sharmistha Nitschke, Felix Minassian, Berge A.