Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Title:
Targeting Gys1 with AAV‐SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models
Author:
Gumusgoz, Emrah Guisso, Dikran R Kasiri, Sahba Wu, Jun Dear, Matthew Verhalen, Brandy Nitschke, Silvia Mitra, Sharmistha Nitschke, Felix Minassian, Berge A.
Appeared in:
Neurotherapeutics
Paging:
Volume 18 () nr. 2 pages 1414-1425
Year:
2021
Contents:
Publisher:
The American Society for Experimental NeuroTherapeutics, Inc.