| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A Combined In Vivo HSC Transduction/Selection Approach Results in Efficient and Stable Gene Expression in Peripheral Blood Cells in Mice
|
Wang, Hongjie
|
|
2018
|
8 |
C |
p. 52-64
|
artikel
|
| 2 |
A Humoral Immune Response Alters the Distribution of Enzyme Replacement Therapy in Murine Mucopolysaccharidosis Type I
|
Le, Steven Q.
|
|
2018
|
8 |
C |
p. 42-51
|
artikel
|
| 3 |
Analyzing the Genotoxicity of Retroviral Vectors in Hematopoietic Cell Gene Therapy
|
Biasco, Luca
|
|
2018
|
8 |
C |
p. 21-30
|
artikel
|
| 4 |
A Nonhuman Primate Transplantation Model to Evaluate Hematopoietic Stem Cell Gene Editing Strategies for β-Hemoglobinopathies
|
Humbert, Olivier
|
|
2018
|
8 |
C |
p. 75-86
|
artikel
|
| 5 |
A Rapamycin-Based GMP-Compatible Process for the Isolation and Expansion of Regulatory T Cells for Clinical Trials
|
Fraser, Henrieta
|
|
2018
|
8 |
C |
p. 198-209
|
artikel
|
| 6 |
Detection of Replication Competent Lentivirus Using a qPCR Assay for VSV-G
|
Skrdlant, Lindsey M.
|
|
2018
|
8 |
C |
p. 1-7
|
artikel
|
| 7 |
Emerging Issues in AAV-Mediated In Vivo Gene Therapy
|
Colella, Pasqualina
|
|
2018
|
8 |
C |
p. 87-104
|
artikel
|
| 8 |
Enhanced Expression of Anti-CD19 Chimeric Antigen Receptor in piggyBac Transposon-Engineered T Cells
|
Morita, Daisuke
|
|
2018
|
8 |
C |
p. 131-140
|
artikel
|
| 9 |
Exploring Cytotoxic mRNAs as a Novel Class of Anti-cancer Biotherapeutics
|
Hirschberger, Kristin
|
|
2018
|
8 |
C |
p. 141-151
|
artikel
|
| 10 |
Improved Expansion and In Vivo Function of Patient T Cells by a Serum-free Medium
|
Medvec, Andrew R.
|
|
2018
|
8 |
C |
p. 65-74
|
artikel
|
| 11 |
Interactions between Retroviruses and the Host Cell Genome
|
Poletti, Valentina
|
|
2018
|
8 |
C |
p. 31-41
|
artikel
|
| 12 |
Nonclinical Safety Evaluation of scAAV8-RLBP1 for Treatment of RLBP1 Retinitis Pigmentosa
|
MacLachlan, Timothy K.
|
|
2018
|
8 |
C |
p. 105-120
|
artikel
|
| 13 |
Pharmacology of Recombinant Adeno-associated Virus Production
|
Penaud-Budloo, Magalie
|
|
2018
|
8 |
C |
p. 166-180
|
artikel
|
| 14 |
Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
|
Yadak, Rana
|
|
2018
|
8 |
C |
p. 152-165
|
artikel
|
| 15 |
Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD
|
Wallace, Lindsay M.
|
|
2018
|
8 |
C |
p. 121-130
|
artikel
|
| 16 |
Safety and Efficacy of AAV Retrograde Pancreatic Ductal Gene Delivery in Normal and Pancreatic Cancer Mice
|
Quirin, Kayla A.
|
|
2018
|
8 |
C |
p. 8-20
|
artikel
|
| 17 |
The Pharmacology of Gene and Cell Therapy
|
Conlon, Thomas J.
|
|
2018
|
8 |
C |
p. 181-182
|
artikel
|
| 18 |
The Pharmacology of T Cell Therapies
|
Milone, Michael C.
|
|
2018
|
8 |
C |
p. 210-221
|
artikel
|
| 19 |
Toxicology and Biodistribution: The Clinical Value of Animal Biodistribution Studies
|
Silva Lima, Beatriz
|
|
2018
|
8 |
C |
p. 183-197
|
artikel
|
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