Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
Titel:
Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
Auteur:
Yadak, Rana Cabrera-Pérez, Raquel Torres-Torronteras, Javier Bugiani, Marianna Haeck, Joost C. Huston, Marshall W. Bogaerts, Elly Goffart, Steffi Jacobs, Edwin H. Stok, Merel Leonardelli, Lorena Biasco, Luca Verdijk, Robert M. Bernsen, Monique R. Ruijter, George Martí, Ramon Wagemaker, Gerard van Til, Niek P. de Coo, Irenaeus F.M.