| no |
title |
author |
magazine |
year |
volume |
issue |
page(s) |
type |
| 1 |
Accelerating clinical-scale production of BCMA CAR T cells with defined maturation stages
|
Joedicke, Jara J.
|
|
|
24 |
C |
p. 181-198
|
article
|
| 2 |
A comprehensive preclinical study supporting clinical trial of oncolytic chimeric poxvirus CF33-hNIS-anti-PD-L1 to treat breast cancer
|
Chaurasiya, Shyambabu
|
|
|
24 |
C |
p. 102-116
|
article
|
| 3 |
Assessment of genome packaging in AAVs using Orbitrap-based charge-detection mass spectrometry
|
Wörner, Tobias P.
|
|
|
24 |
C |
p. 40-47
|
article
|
| 4 |
A universal strategy for AAV delivery of base editors to correct genetic point mutations in neonatal PKU mice
|
Zhou, Lifang
|
|
|
24 |
C |
p. 230-240
|
article
|
| 5 |
Characterization of AAV-mediated dorsal root ganglionopathy
|
Buss, Nicholas
|
|
|
24 |
C |
p. 342-354
|
article
|
| 6 |
Clinically relevant T cell expansion media activate distinct metabolic programs uncoupled from cellular function
|
MacPherson, Sarah
|
|
|
24 |
C |
p. 380-393
|
article
|
| 7 |
Comparison of highly pure rAAV9 vector stocks produced in suspension by PEI transfection or HSV infection reveals striking quantitative and qualitative differences
|
Trivedi, Prasad D.
|
|
|
24 |
C |
p. 154-170
|
article
|
| 8 |
Confirmatory detection of neutralizing antibodies to AAV gene therapy using a cell-based transduction inhibition assay
|
Kasprzyk, Theresa
|
|
|
24 |
C |
p. 222-229
|
article
|
| 9 |
Consensus guidelines for the validation of qRT-PCR assays in clinical research by the CardioRNA consortium
|
de Gonzalo-Calvo, David
|
|
|
24 |
C |
p. 171-180
|
article
|
| 10 |
CRISPR-Cas9-mediated gene disruption of HIV-1 co-receptors confers broad resistance to infection in human T cells and humanized mice
|
Li, Shasha
|
|
|
24 |
C |
p. 321-331
|
article
|
| 11 |
Delivery of non-viral naked DNA vectors to liver in small weaned pigs by hydrodynamic retrograde intrabiliary injection
|
Chan, Tatjana
|
|
|
24 |
C |
p. 268-279
|
article
|
| 12 |
Delivery of nVEGFi using AAV8 for the treatment of neovascular age-related macular degeneration
|
She, Kaiqin
|
|
|
24 |
C |
p. 210-221
|
article
|
| 13 |
Differential T cell immune responses to deamidated adeno-associated virus vector
|
Bing, So Jin
|
|
|
24 |
C |
p. 255-267
|
article
|
| 14 |
Engineered extracellular vesicles directed to the spike protein inhibit SARS-CoV-2
|
Scott, Tristan A.
|
|
|
24 |
C |
p. 355-366
|
article
|
| 15 |
High concordance of ELISA and neutralization assays allows for the detection of antibodies to individual AAV serotypes
|
Gardner, Matthew R.
|
|
|
24 |
C |
p. 199-206
|
article
|
| 16 |
Inducible caspase-9 suicide gene under control of endogenous oct4 to safeguard mouse and human pluripotent stem cell therapy
|
Liu, Yang
|
|
|
24 |
C |
p. 332-341
|
article
|
| 17 |
Intracellular RNase activity dampens zinc finger nuclease-mediated gene editing in hematopoietic stem and progenitor cells
|
Peterson, Christopher W.
|
|
|
24 |
C |
p. 30-39
|
article
|
| 18 |
In vivo optogenetic stimulation of the primate retina activates the visual cortex after long-term transduction
|
Chaffiol, Antoine
|
|
|
24 |
C |
p. 1-10
|
article
|
| 19 |
In vivo overexpression of frataxin causes toxicity mediated by iron-sulfur cluster deficiency
|
Huichalaf, Claudia
|
|
|
24 |
C |
p. 367-378
|
article
|
| 20 |
Long-Term Metabolic Correction of Phenylketonuria by AAV-Delivered Phenylalanine Amino Lyase
|
Tao, Rui
|
|
|
24 |
C |
p. 379
|
article
|
| 21 |
miRNA-mediated control of exogenous OCT4 during mesenchymal-epithelial transition increases measles vector reprogramming efficiency
|
Rallabandi, Ramya
|
|
|
24 |
C |
p. 48-61
|
article
|
| 22 |
Molecular analysis of AAV5-hFVIII-SQ vector-genome-processing kinetics in transduced mouse and nonhuman primate livers
|
Sihn, Choong-Ryoul
|
|
|
24 |
C |
p. 142-153
|
article
|
| 23 |
Monitoring CAR T cell generation with a CD8-targeted lentiviral vector by single-cell transcriptomics
|
Charitidis, Filippos T.
|
|
|
24 |
C |
p. 207-209
|
article
|
| 24 |
Novel human liver-tropic AAV variants define transferable domains that markedly enhance the human tropism of AAV7 and AAV8
|
Cabanes-Creus, Marti
|
|
|
24 |
C |
p. 88-101
|
article
|
| 25 |
Preclinical assessment of an optimized AAV-FVIII vector in mice and non-human primates for the treatment of hemophilia A
|
Elkouby, Liron
|
|
|
24 |
C |
p. 20-29
|
article
|
| 26 |
Prednisolone reduces the interferon response to AAV in cynomolgus macaques and may increase liver gene expression
|
Wang, Lili
|
|
|
24 |
C |
p. 292-305
|
article
|
| 27 |
Preventing packaging of translatable P5-associated DNA contaminants in recombinant AAV vector preps
|
Brimble, Mark A.
|
|
|
24 |
C |
p. 280-291
|
article
|
| 28 |
Promoter considerations in the design of lentiviral vectors for use in treating lysosomal storage diseases
|
Rintz, Estera
|
|
|
24 |
C |
p. 71-87
|
article
|
| 29 |
Rapid, accurate mapping of transgene integration in viable rhesus macaque embryos using enhanced-specificity tagmentation-assisted PCR
|
Ryu, Junghyun
|
|
|
24 |
C |
p. 241-254
|
article
|
| 30 |
RNA-seq analysis of the human surfactant air-liquid interface culture reveals alveolar type II cell-like transcriptome
|
Munis, Altar M.
|
|
|
24 |
C |
p. 62-70
|
article
|
| 31 |
Safe and efficient in vivo hematopoietic stem cell transduction in nonhuman primates using HDAd5/35++ vectors
|
Li, Chang
|
|
|
24 |
C |
p. 127-141
|
article
|
| 32 |
Systemic and local immune responses to intraocular AAV vector administration in non-human primates
|
Ail, Divya
|
|
|
24 |
C |
p. 306-316
|
article
|
| 33 |
Thank you to our 2021 reviewers
|
|
|
|
24 |
C |
p. 317-320
|
article
|
| 34 |
The sodium/glucose cotransporters as potential therapeutic targets for CF lung diseases revealed by human lung organoid swelling assay
|
Hirai, Hiroyuki
|
|
|
24 |
C |
p. 11-19
|
article
|
| 35 |
VikAD, a Vika site-specific recombinase-based system for efficient and scalable helper-dependent adenovirus production
|
Phillips, Stacia
|
|
|
24 |
C |
p. 117-126
|
article
|
Journal description