Preclinical assessment of an optimized AAV-FVIII vector in mice and non-human primates for the treatment of hemophilia A
Titel:
Preclinical assessment of an optimized AAV-FVIII vector in mice and non-human primates for the treatment of hemophilia A
Auteur:
Elkouby, Liron Armour, Sean M. Toso, Raffaella DiPietro, Marti Davidson, Robert J. Nguyen, Giang N. Willet, Mallory Kutza, Stephanie Silverberg, Joseph Frick, Jennifer Crosariol, Marco Wang, Yuhuan Wang, Chuansong High, Katherine A. Sabatino, Denise E. Anguela, Xavier M.