| no |
title |
author |
magazine |
year |
volume |
issue |
page(s) |
type |
| 1 |
AAV-8 and AAV-9 Vectors Cooperate with Serum Proteins Differently Than AAV-1 and AAV-6
|
Denard, Jérôme
|
|
|
10 |
C |
p. 291-302
|
article
|
| 2 |
A Bovine Adenoviral Vector-Based H5N1 Influenza -Vaccine Provides Enhanced Immunogenicity and Protection at a Significantly Low Dose
|
Sayedahmed, Ekramy E.
|
|
|
10 |
C |
p. 210-222
|
article
|
| 3 |
Accurate Titration of Infectious AAV Particles Requires Measurement of Biologically Active Vector Genomes and Suitable Controls
|
François, Achille
|
|
|
10 |
C |
p. 223-236
|
article
|
| 4 |
A Direct Comparison of IV and ICV Delivery Methods for Gene Replacement Therapy in a Mouse Model of SMARD1
|
Shababi, Monir
|
|
|
10 |
C |
p. 348-360
|
article
|
| 5 |
A Library-Based Screening Strategy for the Identification of DARPins as Ligands for Receptor-Targeted AAV and Lentiviral Vectors
|
Hartmann, Jessica
|
|
|
10 |
C |
p. 128-143
|
article
|
| 6 |
An Introduction to the Analysis of Single-Cell RNA-Sequencing Data
|
AlJanahi, Aisha A.
|
|
|
10 |
C |
p. 189-196
|
article
|
| 7 |
An Isolated Limb Infusion Method Allows for Broad Distribution of rAAVrh74.MCK.GALGT2 to Leg Skeletal Muscles in the Rhesus Macaque
|
Xu, Rui
|
|
|
10 |
C |
p. 89-104
|
article
|
| 8 |
An Observational Study from Long-Term AAV Re-administration in Two Hemophilia Dogs
|
Sun, Junjiang
|
|
|
10 |
C |
p. 257-267
|
article
|
| 9 |
A Nontoxic Transduction Enhancer Enables Highly Efficient Lentiviral Transduction of Primary Murine T Cells and Hematopoietic Stem Cells
|
Delville, Marianne
|
|
|
10 |
C |
p. 341-347
|
article
|
| 10 |
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype
|
Weber, Leslie
|
|
|
10 |
C |
p. 268-280
|
article
|
| 11 |
A Recombinant Baculovirus Efficiently Generates Recombinant Adeno-Associated Virus Vectors in Cultured Insect Cells and Larvae
|
Wu, Yang
|
|
|
10 |
C |
p. 38-47
|
article
|
| 12 |
Bioengineered Viral Platform for Intramuscular Passive Vaccine Delivery to Human Skeletal Muscle
|
Paulk, Nicole K.
|
|
|
10 |
C |
p. 144-155
|
article
|
| 13 |
Bone-Targeted Alkaline Phosphatase Treatment of Mandibular Bone and Teeth in Lethal Hypophosphatasia via an scAAV8 Vector
|
Ikeue, Ryo
|
|
|
10 |
C |
p. 361-370
|
article
|
| 14 |
Cerebrospinal Fluid-Directed rAAV9-rsATP7A Plus Subcutaneous Copper Histidinate Advance Survival and Outcomes in a Menkes Disease Mouse Model
|
Haddad, Marie Reine
|
|
|
10 |
C |
p. 165-178
|
article
|
| 15 |
Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome
|
Greig, Jenny A.
|
|
|
10 |
C |
p. 237-244
|
article
|
| 16 |
Development of Methods for the Selective Measurement of the Single Amino Acid Exchange Variant Coagulation Factor IX Padua
|
Weber, Alfred
|
|
|
10 |
C |
p. 29-37
|
article
|
| 17 |
Disruption of the BCL11A Erythroid Enhancer Reactivates Fetal Hemoglobin in Erythroid Cells of Patients with β-Thalassemia Major
|
Psatha, Nikoletta
|
|
|
10 |
C |
p. 313-326
|
article
|
| 18 |
Efficient Gene Transfer to the Central Nervous System by Single-Stranded Anc80L65
|
Hudry, Eloise
|
|
|
10 |
C |
p. 197-209
|
article
|
| 19 |
Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice
|
Clarke, Don
|
|
|
10 |
C |
p. 113-127
|
article
|
| 20 |
GMP Production and Scale-Up of Adherent Neural Stem Cells with a Quantum Cell Expansion System
|
Tirughana, Revathiswari
|
|
|
10 |
C |
p. 48-56
|
article
|
| 21 |
Helper-free Production of Laboratory Grade AAV and Purification by Iodixanol Density Gradient Centrifugation
|
Crosson, Sean M.
|
|
|
10 |
C |
p. 1-7
|
article
|
| 22 |
Impact of Dental Pulp Stem Cells Overexpressing Hepatocyte Growth Factor after Cerebral Ischemia/Reperfusion in Rats
|
Sowa, Kota
|
|
|
10 |
C |
p. 281-290
|
article
|
| 23 |
Inferring Novel Tumor Suppressor Genes with a Protein-Protein Interaction Network and Network Diffusion Algorithms
|
Chen, Lei
|
|
|
10 |
C |
p. 57-67
|
article
|
| 24 |
Integrated Human Evaluation of the Lysophosphatidic Acid Pathway as a Novel Therapeutic Target in Atherosclerosis
|
Aldi, Silvia
|
|
|
10 |
C |
p. 17-28
|
article
|
| 25 |
Lentivector Producer Cell Lines with Stably Expressed Vesiculovirus Envelopes
|
Tijani, Maha
|
|
|
10 |
C |
p. 303-312
|
article
|
| 26 |
Prevalence of Pre-existing Antibodies to CRISPR-Associated Nuclease Cas9 in the USA Population
|
Simhadri, Vijaya L.
|
|
|
10 |
C |
p. 105-112
|
article
|
| 27 |
Screening Clinical Cell Products for Replication Competent Retrovirus: The National Gene Vector Biorepository Experience
|
Cornetta, Kenneth
|
|
|
10 |
C |
p. 371-378
|
article
|
| 28 |
Targeting Heparan Sulfate Proteoglycans as a Novel Therapeutic Strategy for Mucopolysaccharidoses
|
De Pasquale, Valeria
|
|
|
10 |
C |
p. 8-16
|
article
|
| 29 |
Targeting Root Cause by Systemic scAAV9-hIDS Gene Delivery: Functional Correction and Reversal of Severe MPS II in Mice
|
Fu, Haiyan
|
|
|
10 |
C |
p. 327-340
|
article
|
| 30 |
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques
|
Hordeaux, Juliette
|
|
|
10 |
C |
p. 79-88
|
article
|
| 31 |
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques
|
Hordeaux, Juliette
|
|
|
10 |
C |
p. 68-78
|
article
|
| 32 |
Ultrasound-Mediated Gene Therapy in Swine Livers Using Single-Element, Multi-lensed, High-Intensity Ultrasound Transducers
|
Noble-Vranish, Misty L.
|
|
|
10 |
C |
p. 179-188
|
article
|
| 33 |
UM171 Enhances Lentiviral Gene Transfer and Recovery of Primitive Human Hematopoietic Cells
|
Ngom, Mor
|
|
|
10 |
C |
p. 156-164
|
article
|
| 34 |
Use of Precision-Cut Lung Slices as an Ex Vivo Tool for Evaluating Viruses and Viral Vectors for Gene and Oncolytic Therapy
|
Rosales Gerpe, María C.
|
|
|
10 |
C |
p. 245-256
|
article
|
Journal description