Cerebrospinal Fluid-Directed rAAV9-rsATP7A Plus Subcutaneous Copper Histidinate Advance Survival and Outcomes in a Menkes Disease Mouse Model
Titel:
Cerebrospinal Fluid-Directed rAAV9-rsATP7A Plus Subcutaneous Copper Histidinate Advance Survival and Outcomes in a Menkes Disease Mouse Model
Auteur:
Haddad, Marie Reine Choi, Eun-Young Zerfas, Patricia M. Yi, Ling Martinelli, Diego Sullivan, Patricia Goldstein, David S. Centeno, Jose A. Brinster, Lauren R. Ralle, Martina Kaler, Stephen G.