| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A Novel Single-Strand RNAi Therapeutic Agent Targeting the (Pro)renin Receptor Suppresses Ocular Inflammation
|
Kanda, Atsuhiro
|
|
2017
|
7 |
C |
p. 116-126
11 p.
|
artikel
|
| 2 |
Antisense Oligonucleotides Promote Exon Inclusion and Correct the Common c.-32-13T>G GAA Splicing Variant in Pompe Disease
|
van der Wal, Erik
|
|
2017
|
7 |
C |
p. 90-100
11 p.
|
artikel
|
| 3 |
ATG7 Overexpression Is Crucial for Tumorigenic Growth of Bladder Cancer In Vitro and In Vivo by Targeting the ETS2/miRNA196b/FOXO1/p27 Axis
|
Zhu, Junlan
|
|
2017
|
7 |
C |
p. 299-313
15 p.
|
artikel
|
| 4 |
Broad-Spectrum Inhibition of Respiratory Virus Infection by MicroRNA Mimics Targeting p38 MAPK Signaling
|
McCaskill, Jana L.
|
|
2017
|
7 |
C |
p. 256-266
11 p.
|
artikel
|
| 5 |
Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System
|
Lattanzi, Annalisa
|
|
2017
|
7 |
C |
p. 11-19
9 p.
|
artikel
|
| 6 |
CRISPR/Cas9-Directed Reassignment of the GATA1 Initiation Codon in K562 Cells to Recapitulate AML in Down Syndrome
|
Bloh, Kevin M.
|
|
2017
|
7 |
C |
p. 288-298
11 p.
|
artikel
|
| 7 |
CRISPR/Cas9-loxP-Mediated Gene Editing as a Novel Site-Specific Genetic Manipulation Tool
|
Yang, Fayu
|
|
2017
|
7 |
C |
p. 378-386
9 p.
|
artikel
|
| 8 |
CRISPR/Cas9-Mediated Genome Editing Corrects Dystrophin Mutation in Skeletal Muscle Stem Cells in a Mouse Model of Muscle Dystrophy
|
Zhu, Pei
|
|
2017
|
7 |
C |
p. 31-41
11 p.
|
artikel
|
| 9 |
CRISPR/Cas9-Mediated Three Nucleotide Insertion Corrects a Deletion Mutation in MRP1/ABCC1 and Restores Its Proper Folding and Function
|
Xu, Qinqin
|
|
2017
|
7 |
C |
p. 429-438
10 p.
|
artikel
|
| 10 |
CRISPR/Cas9: Transcending the Reality of Genome Editing
|
Chira, Sergiu
|
|
2017
|
7 |
C |
p. 211-222
12 p.
|
artikel
|
| 11 |
Efficacy of Postnatal In Vivo Nonsense Suppression Therapy in a Pax6 Mouse Model of Aniridia
|
Wang, Xia
|
|
2017
|
7 |
C |
p. 417-428
12 p.
|
artikel
|
| 12 |
Efficient SMN Rescue following Subcutaneous Tricyclo-DNA Antisense Oligonucleotide Treatment
|
Robin, Valérie
|
|
2017
|
7 |
C |
p. 81-89
9 p.
|
artikel
|
| 13 |
Emerging Roles of circRNA Related to the Mechanical Stress in Human Cartilage Degradation of Osteoarthritis
|
Liu, Qiang
|
|
2017
|
7 |
C |
p. 223-230
8 p.
|
artikel
|
| 14 |
Engineering Next-Generation BET-Independent MLV Vectors for Safer Gene Therapy
|
El Ashkar, Sara
|
|
2017
|
7 |
C |
p. 231-245
15 p.
|
artikel
|
| 15 |
Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models
|
Moore, Lauren R.
|
|
2017
|
7 |
C |
p. 200-210
11 p.
|
artikel
|
| 16 |
Evaluation of MYBPC3 trans-Splicing and Gene Replacement as Therapeutic Options in Human iPSC-Derived Cardiomyocytes
|
Prondzynski, Maksymilian
|
|
2017
|
7 |
C |
p. 475-486
12 p.
|
artikel
|
| 17 |
Exosome Mediated Delivery of miR-124 Promotes Neurogenesis after Ischemia
|
Yang, Jialei
|
|
2017
|
7 |
C |
p. 278-287
10 p.
|
artikel
|
| 18 |
Expression of Herpes Simplex Virus Thymidine Kinase/Ganciclovir by RNA Trans-Splicing Induces Selective Killing of HIV-Producing Cells
|
Ingemarsdotter, Carin K.
|
|
2017
|
7 |
C |
p. 140-154
15 p.
|
artikel
|
| 19 |
Fluorinated Nucleotide Modifications Modulate Allele Selectivity of SNP-Targeting Antisense Oligonucleotides
|
Østergaard, Michael E.
|
|
2017
|
7 |
C |
p. 20-30
11 p.
|
artikel
|
| 20 |
Further Characterization of the Bifunctional HIV Entry Inhibitor sCD4-FIT45
|
Falkenhagen, Alexander
|
|
2017
|
7 |
C |
p. 387-395
9 p.
|
artikel
|
| 21 |
GAA Deficiency in Pompe Disease Is Alleviated by Exon Inclusion in iPSC-Derived Skeletal Muscle Cells
|
van der Wal, Erik
|
|
2017
|
7 |
C |
p. 101-115
15 p.
|
artikel
|
| 22 |
Gold Nanoparticles for BCR-ABL1 Gene Silencing: Improving Tyrosine Kinase Inhibitor Efficacy in Chronic Myeloid Leukemia
|
Vinhas, Raquel
|
|
2017
|
7 |
C |
p. 408-416
9 p.
|
artikel
|
| 23 |
Identification of Novel Fibrosis Modifiers by In Vivo siRNA Silencing
|
Vollmann, Elisabeth H.
|
|
2017
|
7 |
C |
p. 314-323
10 p.
|
artikel
|
| 24 |
Inhibition of Mef2a Enhances Neovascularization via Post-transcriptional Regulation of 14q32 MicroRNAs miR-329 and miR-494
|
Welten, Sabine M.J.
|
|
2017
|
7 |
C |
p. 61-70
10 p.
|
artikel
|
| 25 |
iRNA-PseColl: Identifying the Occurrence Sites of Different RNA Modifications by Incorporating Collective Effects of Nucleotides into PseKNC
|
Feng, Pengmian
|
|
2017
|
7 |
C |
p. 155-163
9 p.
|
artikel
|
| 26 |
Light-Triggerable Liposomes for Enhanced Endolysosomal Escape and Gene Silencing in PC12 Cells
|
Chen, Wenjie
|
|
2017
|
7 |
C |
p. 366-377
12 p.
|
artikel
|
| 27 |
Low-Dose Gene Therapy for Murine PKU Using Episomal Naked DNA Vectors Expressing PAH from Its Endogenous Liver Promoter
|
Grisch-Chan, Hiu Man
|
|
2017
|
7 |
C |
p. 339-349
11 p.
|
artikel
|
| 28 |
2L-piRNA: A Two-Layer Ensemble Classifier for Identifying Piwi-Interacting RNAs and Their Function
|
Liu, Bin
|
|
2017
|
7 |
C |
p. 267-277
11 p.
|
artikel
|
| 29 |
Mathematical Modeling: A Tool for Optimization of Lipid Nanoparticle-Mediated Delivery of siRNA
|
Mihaila, Radu
|
|
2017
|
7 |
C |
p. 246-255
10 p.
|
artikel
|
| 30 |
MicroRNA-146a-5p Limits Elevated TGF-β Signal during Cell Senescence
|
Min, Seung-Ki
|
|
2017
|
7 |
C |
p. 335-338
4 p.
|
artikel
|
| 31 |
MiR-375 and Doxorubicin Co-delivered by Liposomes for Combination Therapy of Hepatocellular Carcinoma
|
Fan, Yin-Ping
|
|
2017
|
7 |
C |
p. 181-189
9 p.
|
artikel
|
| 32 |
Mir30c Is Involved in Diabetic Cardiomyopathy through Regulation of Cardiac Autophagy via BECN1
|
Chen, Chen
|
|
2017
|
7 |
C |
p. 127-139
13 p.
|
artikel
|
| 33 |
miR-1290 Is a Biomarker in DNA-Mismatch-Repair-Deficient Colon Cancer and Promotes Resistance to 5-Fluorouracil by Directly Targeting hMSH2
|
Ye, Ling
|
|
2017
|
7 |
C |
p. 453-464
12 p.
|
artikel
|
| 34 |
Optimizing the DNA Donor Template for Homology-Directed Repair of Double-Strand Breaks
|
Song, Fei
|
|
2017
|
7 |
C |
p. 53-60
8 p.
|
artikel
|
| 35 |
Periostin-Binding DNA Aptamer Treatment Ameliorates Peritoneal Dialysis-Induced Peritoneal Fibrosis
|
Nam, Bo Young
|
|
2017
|
7 |
C |
p. 396-407
12 p.
|
artikel
|
| 36 |
Safe and Efficient Silencing with a Pol II, but Not a Pol lII, Promoter Expressing an Artificial miRNA Targeting Human Huntingtin
|
Pfister, Edith L.
|
|
2017
|
7 |
C |
p. 324-334
11 p.
|
artikel
|
| 37 |
Stimuli-Responsive Mesoporous Silica NPs as Non-viral Dual siRNA/Chemotherapy Carriers for Triple Negative Breast Cancer
|
Darvishi, Behrad
|
|
2017
|
7 |
C |
p. 164-180
17 p.
|
artikel
|
| 38 |
Sustained Inhibition of HBV Replication In Vivo after Systemic Injection of AAVs Encoding Artificial Antiviral Primary MicroRNAs
|
Maepa, Mohube Betty
|
|
2017
|
7 |
C |
p. 190-199
10 p.
|
artikel
|
| 39 |
Targeted Multifunctional Lipid ECO Plasmid DNA Nanoparticles as Efficient Non-viral Gene Therapy for Leber’s Congenital Amaurosis
|
Sun, Da
|
|
2017
|
7 |
C |
p. 42-52
11 p.
|
artikel
|
| 40 |
Targeting DMPK with Antisense Oligonucleotide Improves Muscle Strength in Myotonic Dystrophy Type 1 Mice
|
Jauvin, Dominic
|
|
2017
|
7 |
C |
p. 465-474
10 p.
|
artikel
|
| 41 |
Tat-haFGF14–154 Upregulates ADAM10 to Attenuate the Alzheimer Phenotype of APP/PS1 Mice through the PI3K-CREB-IRE1α/XBP1 Pathway
|
Meng, Tian
|
|
2017
|
7 |
C |
p. 439-452
14 p.
|
artikel
|
| 42 |
The Formation of Nanoparticles between Small Interfering RNA and Amphipathic Cell-Penetrating Peptides
|
Pärnaste, Ly
|
|
2017
|
7 |
C |
p. 1-10
10 p.
|
artikel
|
| 43 |
Transcriptome-wide Investigation of mRNA/circRNA in miR-184 and Its r.57c > u Mutant Type Treatment of Human Lens Epithelial Cells
|
Luo, Yueqiu
|
|
2017
|
7 |
C |
p. 71-80
10 p.
|
artikel
|
| 44 |
Translation of Angiotensin-Converting Enzyme 2 upon Liver- and Lung-Targeted Delivery of Optimized Chemically Modified mRNA
|
Schrom, Eva
|
|
2017
|
7 |
C |
p. 350-365
16 p.
|
artikel
|
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