Evaluation of MYBPC3 trans-Splicing and Gene Replacement as Therapeutic Options in Human iPSC-Derived Cardiomyocytes
Titel:
Evaluation of MYBPC3 trans-Splicing and Gene Replacement as Therapeutic Options in Human iPSC-Derived Cardiomyocytes
Auteur:
Prondzynski, Maksymilian Krämer, Elisabeth Laufer, Sandra D. Shibamiya, Aya Pless, Ole Flenner, Frederik Müller, Oliver J. Münch, Julia Redwood, Charles Hansen, Arne Patten, Monica Eschenhagen, Thomas Mearini, Giulia Carrier, Lucie