| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV-RNAi constructs promote DRG toxicity
|
Xie, Jun
|
|
|
33 |
1 |
p. 21-22
|
artikel
|
| 2 |
Amelioration of metabolic and behavioral defects through base editing in the PahR408W phenylketonuria mouse model
|
Yin, Shuming
|
|
|
33 |
1 |
p. 119-132
|
artikel
|
| 3 |
A novel CD71 Centyrin:Gys1 siRNA conjugate reduces glycogen synthesis and glycogen levels in a mouse model of Pompe disease
|
Holt, Bryce D.
|
|
|
33 |
1 |
p. 235-248
|
artikel
|
| 4 |
Anti-microRNA-378a Enhances Wound Healing Process by Upregulating Integrin Beta-3 and Vimentin
|
Li, Haoran
|
|
|
33 |
1 |
p. 415
|
artikel
|
| 5 |
ARI0003: Co-transduced CD19/BCMA dual-targeting CAR-T cells for the treatment of non-Hodgkin lymphoma
|
Bachiller, Mireia
|
|
|
33 |
1 |
p. 317-335
|
artikel
|
| 6 |
A small TAT-TrkB peptide prevents BDNF receptor cleavage and restores synaptic physiology in Alzheimer’s disease
|
Fonseca-Gomes, João
|
|
|
33 |
1 |
p. 421
|
artikel
|
| 7 |
Balancing efficacy and safety in lentiviral vector-mediated hematopoietic stem cell gene therapy
|
Montini, Eugenio
|
|
|
33 |
1 |
p. 6-8
|
artikel
|
| 8 |
Biologics-based technologies for highly efficient and targeted RNA delivery
|
Kostyusheva, Anastasiya
|
|
|
33 |
1 |
p. 168-183
|
artikel
|
| 9 |
CD137-expressing regulatory T cells in cancer and autoimmune diseases
|
Lee, Kang Yi
|
|
|
33 |
1 |
p. 51-70
|
artikel
|
| 10 |
Choosing the right double-barreled gun: ARI0003 takes aim at lymphoma by targeting both CD19 and BCMA
|
Rampotas, Alexandros
|
|
|
33 |
1 |
p. 23-25
|
artikel
|
| 11 |
Combination with oxaliplatin improves abscopal effect of oncolytic virotherapy through reorganization of intratumoral macrophages
|
Tomita, Kyoko
|
|
|
33 |
1 |
p. 401-414
|
artikel
|
| 12 |
C-reactive protein in diabetic kidney disease: A new therapeutic avenue?
|
Cai, Juan
|
|
|
33 |
1 |
p. 26-27
|
artikel
|
| 13 |
C-reactive protein promotes diabetic kidney disease via Smad3-mediated NLRP3 inflammasome activation
|
Wang, Yifan
|
|
|
33 |
1 |
p. 263-278
|
artikel
|
| 14 |
CRISPR targeting of mmu-miR-21a through a single adeno-associated virus vector prolongs survival of glioblastoma-bearing mice
|
Nieland, Lisa
|
|
|
33 |
1 |
p. 133-151
|
artikel
|
| 15 |
Critical role of TPRN rings in the stereocilia for hearing
|
Qi, Jieyu
|
|
|
33 |
1 |
p. 419-420
|
artikel
|
| 16 |
Cutting through the stones: Unlocking therapeutic potential with gene editing tools for primary hyperoxaluria type 1
|
Schneller, Jessica
|
|
|
33 |
1 |
p. 11-13
|
artikel
|
| 17 |
Debulking influenza and herpes simplex virus strains by a wide-spectrum anti-viral protein formulated in clinical grade chewing gum
|
Daniell, Henry
|
|
|
33 |
1 |
p. 184-200
|
artikel
|
| 18 |
Dorsal root ganglion toxicity after AAV intra-CSF delivery of a RNAi expression construct into non-human primates and mice
|
Hawley, Zachary C.E.
|
|
|
33 |
1 |
p. 215-234
|
artikel
|
| 19 |
Efficient and safe in vivo treatment of primary hyperoxaluria type 1 via LNP-CRISPR-Cas9-mediated glycolate oxidase disruption
|
Jiang, Yanhong
|
|
|
33 |
1 |
p. 104-118
|
artikel
|
| 20 |
Efficient and safe in vivo treatment of primary hyperoxaluria type 1 via LNP-CRISPR-Cas9-mediated glycolate oxidase disruption
|
Jiang, Yanhong
|
|
|
33 |
1 |
p. 417-418
|
artikel
|
| 21 |
Expanding nucleic acid-encoded medicine
|
Chai, Dafei
|
|
|
33 |
1 |
p. 16-17
|
artikel
|
| 22 |
Getting the host antiviral machinery back on track: Targeting viral suppressors of RNA interference
|
Gao, Wenqing
|
|
|
33 |
1 |
p. 18-20
|
artikel
|
| 23 |
Hypermethylation and suppression of microRNA219a-2 activates the ALDH1L2/GSH/PAI-1 pathway for fibronectin degradation in renal fibrosis
|
Wei, Qingqing
|
|
|
33 |
1 |
p. 249-262
|
artikel
|
| 24 |
In this issue
|
|
|
|
33 |
1 |
p. 5
|
artikel
|
| 25 |
Lipid nanoparticle delivery of TALEN mRNA targeting LPA causes gene disruption and plasma lipoprotein(a) reduction in transgenic mice
|
Garcia, Daniel A.
|
|
|
33 |
1 |
p. 90-103
|
artikel
|
| 26 |
miRNA discovery to therapy: The field is sufficiently mature to assess the value of miRNA-based therapeutics
|
Baker, Andrew H.
|
|
|
33 |
1 |
p. 3-4
|
artikel
|
| 27 |
Modified human mesenchymal stromal/stem cells restore cortical excitability after focal ischemic stroke in rats
|
Klein, Barbara
|
|
|
33 |
1 |
p. 375-400
|
artikel
|
| 28 |
Neuroplasticity therapy using glia-like cells derived from human mesenchymal stem cells for the recovery of cerebral infarction sequelae
|
Lee, Eun Ji
|
|
|
33 |
1 |
p. 356-374
|
artikel
|
| 29 |
Novel epigenetic cross-talk down-regulates kidney fibrosis after injury
|
Sheikh-Hamad, David
|
|
|
33 |
1 |
p. 14-15
|
artikel
|
| 30 |
Novel insights into the ROCK-JAK-STAT signaling pathway in upper respiratory tract infections and neurodegenerative diseases
|
Li, Jiaxuan
|
|
|
33 |
1 |
p. 32-50
|
artikel
|
| 31 |
Orthogonal transcriptional modulation and gene editing using multiple CRISPR-Cas systems
|
Broksø, Amalie Dyrelund
|
|
|
33 |
1 |
p. 71-89
|
artikel
|
| 32 |
Proton pump inhibitor attenuates acidic microenvironment to improve the therapeutic effects of MSLN-CAR-T cells on the brain metastasis
|
Zhai, Xuejia
|
|
|
33 |
1 |
p. 336-355
|
artikel
|
| 33 |
Retraction Notice to: Inhibition of Hepatitis C Virus Replication by Intracellular Delivery of Multiple siRNAs by Nanosomes
|
Chandra, Partha K.
|
|
|
33 |
1 |
p. 422
|
artikel
|
| 34 |
Second gene therapy for hemophilia B approved: More answers or questions?
|
Kaczmarek, Radoslaw
|
|
|
33 |
1 |
p. 1-2
|
artikel
|
| 35 |
SNRK modulates mTOR-autophagy pathway for liver lipid homeostasis in MAFLD
|
Lin, Shan
|
|
|
33 |
1 |
p. 279-296
|
artikel
|
| 36 |
SNRK tames mTOR against metabolic dysfunction-associated steatotic liver disease
|
Brunetti-Pierri, Nicola
|
|
|
33 |
1 |
p. 28-29
|
artikel
|
| 37 |
Structure and sequence engineering approaches to improve in vivo expression of nucleic acid-delivered antibodies
|
Helble, Michaela
|
|
|
33 |
1 |
p. 152-167
|
artikel
|
| 38 |
Targeting PD-1+ T cells with small-format immunocytokines enhances IL-12 antitumor activity
|
Silva-Pilipich, Noelia
|
|
|
33 |
1 |
p. 297-316
|
artikel
|
| 39 |
Targeting viral suppressor of RNAi confers anti-coronaviral activity
|
Chen, Jiyao
|
|
|
33 |
1 |
p. 201-214
|
artikel
|
| 40 |
The Circular RNA circSKA3 Binds Integrin β1 to Induce Invadopodium Formation Enhancing Breast Cancer Invasion
|
Du, William W.
|
|
|
33 |
1 |
p. 416
|
artikel
|
| 41 |
Three’s company: Simultaneous trimodal genome engineering using orthologous Cas proteins
|
Brooks, Imogen R.
|
|
|
33 |
1 |
p. 9-10
|
artikel
|
| 42 |
When promising therapies are out of reach: Ethical responsibilities of stakeholders in gene therapy trials for rare disorders
|
Major, Rami M.
|
|
|
33 |
1 |
p. 30-31
|
artikel
|
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