A novel CD71 Centyrin:Gys1 siRNA conjugate reduces glycogen synthesis and glycogen levels in a mouse model of Pompe disease
Titel:
A novel CD71 Centyrin:Gys1 siRNA conjugate reduces glycogen synthesis and glycogen levels in a mouse model of Pompe disease
Auteur:
Holt, Bryce D. Elliott, Samuel J. Meyer, Rebecca Reyes, Daniela O’Neil, Karyn Druzina, Zhanna Kulkarni, Swapnil Thurberg, Beth L. Nadler, Steven G. Pederson, Bartholomew A.