| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV-mediated Stambp gene replacement therapy rescues neurological defects in a mouse model of microcephaly-capillary malformation syndrome
|
Hu, Meixin
|
|
|
32 |
11 |
p. 4095-4107
|
artikel
|
| 2 |
AAV vector-derived elements integrate into Cas9-generated double-strand breaks and disrupt gene transcription
|
Bazick, Hannah O.
|
|
|
32 |
11 |
p. 4122-4137
|
artikel
|
| 3 |
A CD25×TIGIT bispecific antibody induces anti-tumor activity through selective intratumoral Treg cell depletion
|
Wei, Xin
|
|
|
32 |
11 |
p. 4075-4094
|
artikel
|
| 4 |
A chimeric anti-vascularization immunomodulator prevents high-risk corneal transplantation rejection via ex vivo gene therapy
|
Gilger, Brian C.
|
|
|
32 |
11 |
p. 4006-4020
|
artikel
|
| 5 |
Anti-amyloid treatment is broadly effective in neuronopathic mucopolysaccharidoses and synergizes with gene therapy in MPS-IIIA
|
Giaccio, Marianna
|
|
|
32 |
11 |
p. 4108-4121
|
artikel
|
| 6 |
Anti-CLL1 liposome loaded with miR-497-5p and venetoclax as a novel therapeutic strategy in acute myeloid leukemia
|
Pan, Qiaoyu
|
|
|
32 |
11 |
p. 4058-4074
|
artikel
|
| 7 |
Case study of CD19 CAR T therapy in a subject with immune-mediate necrotizing myopathy treated in the RESET-Myositis phase I/II trial
|
Volkov, Jenell
|
|
|
32 |
11 |
p. 3821-3828
|
artikel
|
| 8 |
CasRx-based Wnt activation promotes alveolar regeneration while ameliorating pulmonary fibrosis in a mouse model of lung injury
|
Shen, Shengxi
|
|
|
32 |
11 |
p. 3974-3989
|
artikel
|
| 9 |
Does increased CCL2-mediated immune cell recruitment during mucosal BCG vaccination provide superior protection against TB?
|
Serpa, Gregory
|
|
|
32 |
11 |
p. 3763-3764
|
artikel
|
| 10 |
Endothelial-to-mesenchymal transition enhances permissiveness to AAV vectors in cardiac endothelial cells
|
Volf, Nina
|
|
|
32 |
11 |
p. 3808-3814
|
artikel
|
| 11 |
Engineering memory T cells as a platform for long-term enzyme replacement therapy in lysosomal storage disorders
|
Kleinboehl, Evan W.
|
|
|
32 |
11 |
p. 3865-3878
|
artikel
|
| 12 |
Entering the playing field: Therapy for multiple sulfatase deficiency
|
Dickson, Patricia
|
|
|
32 |
11 |
p. 3756-3757
|
artikel
|
| 13 |
Expanding CAR-engineered cell therapies into autoimmune diseases
|
Green, Shon
|
|
|
32 |
11 |
p. 3768-3769
|
artikel
|
| 14 |
Gene therapy trial lights the way for patients with Leber congenital amaurosis 1
|
Chan, Ying Kai
|
|
|
32 |
11 |
p. 3748-3750
|
artikel
|
| 15 |
GTSE1-driven ZEB1 stabilization promotes pulmonary fibrosis through the epithelial-to-mesenchymal transition
|
Jin, Hee
|
|
|
32 |
11 |
p. 4138-4157
|
artikel
|
| 16 |
Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency
|
Pham, Vi
|
|
|
32 |
11 |
p. 3829-3846
|
artikel
|
| 17 |
Innovative stroke intervention: Harnessing cerebral dopamine neurotrophic factor
|
Hou, Dan
|
|
|
32 |
11 |
p. 3753-3755
|
artikel
|
| 18 |
In this issue
|
|
|
|
32 |
11 |
p. 3747
|
artikel
|
| 19 |
Intranasal vaccination with engineered BCG expressing CCL2 induces a stronger immune barrier against Mycobacterium tuberculosis than BCG
|
Guo, Shaohua
|
|
|
32 |
11 |
p. 3990-4005
|
artikel
|
| 20 |
In vivo neuroregenerative gene therapy to treat neurodegenerative disorders
|
Chen, Gong
|
|
|
32 |
11 |
p. 3770-3771
|
artikel
|
| 21 |
Novel treatment for PXE: Recombinant ENPP1 enzyme therapy
|
Jacobs, Ida Joely
|
|
|
32 |
11 |
p. 3815-3820
|
artikel
|
| 22 |
On RNA-programmable gene modulation as a versatile set of principles targeting muscular dystrophies
|
Capelletti, Sabrina
|
|
|
32 |
11 |
p. 3793-3807
|
artikel
|
| 23 |
Preclinical lentiviral hematopoietic stem cell gene therapy corrects Pompe disease-related muscle and neurological manifestations
|
Yoon, John K.
|
|
|
32 |
11 |
p. 3847-3864
|
artikel
|
| 24 |
Prevention of prostate cancer metastasis by a CRISPR-delivering nanoplatform for interleukin-30 genome editing
|
Fieni, Cristiano
|
|
|
32 |
11 |
p. 3932-3954
|
artikel
|
| 25 |
Single-cell RNA sequencing reveals anti-tumor potency of CD56+ NK cells and CD8+ T cells in humanized mice via PD-1 and TIGIT co-targeting
|
Liu, Wai Nam
|
|
|
32 |
11 |
p. 3895-3914
|
artikel
|
| 26 |
Synergistic integration of mRNA-LNP with CAR-engineered immune cells: Pioneering progress in immunotherapy
|
Chen, Zhaozhao
|
|
|
32 |
11 |
p. 3772-3792
|
artikel
|
| 27 |
TALEN-edited allogeneic inducible dual CAR T cells enable effective targeting of solid tumors while mitigating off-tumor toxicity
|
Dharani, Sonal
|
|
|
32 |
11 |
p. 3915-3931
|
artikel
|
| 28 |
Targeting intratumoral Tregs: The promise of CD25×TIGIT bispecific antibodies in solid tumor therapy
|
Venkatachalapathy, Muthukumaran
|
|
|
32 |
11 |
p. 3758-3760
|
artikel
|
| 29 |
Targeting Rap1b signaling cascades with CDNF: Mitigating platelet activation, plasma oxylipins and reperfusion injury in stroke
|
Wu, Jui-Sheng
|
|
|
32 |
11 |
p. 4021-4044
|
artikel
|
| 30 |
Targeting ROS-sensing Nrf2 potentiates anti-tumor immunity of intratumoral CD8+ T and CAR-T cells
|
Jo, Yuna
|
|
|
32 |
11 |
p. 3879-3894
|
artikel
|
| 31 |
Therapeutic CRISPR epigenome editing of inflammatory receptors in the intervertebral disc
|
Stover, Joshua D.
|
|
|
32 |
11 |
p. 3955-3973
|
artikel
|
| 32 |
Transcriptional orchestration of EMT: Unraveling novel molecular targets in pulmonary fibrosis
|
Bobis-Wozowicz, Sylwia
|
|
|
32 |
11 |
p. 3765-3767
|
artikel
|
| 33 |
Transforming transplantation science: New advanced molecular strategy to overcome corneal graft rejection
|
Al Monla, Reem
|
|
|
32 |
11 |
p. 3751-3752
|
artikel
|
| 34 |
Unveiling the relevance of immune checkpoints for innate and adaptive response to hepatocellular carcinoma using improved model of humanized mice
|
Porgador, Angel
|
|
|
32 |
11 |
p. 3761-3762
|
artikel
|
| 35 |
Urinary Extracellular Vesicles Carrying Klotho Improve the Recovery of Renal Function in an Acute Tubular Injury Model
|
Grange, Cristina
|
|
|
32 |
11 |
p. 4158-4159
|
artikel
|
| 36 |
VSTM2A reverses immunosuppression in colorectal cancer by antagonizing the PD-L1/PD-1 interaction
|
Dong, Yujuan
|
|
|
32 |
11 |
p. 4045-4057
|
artikel
|
| 37 |
VSTM2A reverses immunosuppression in colorectal cancer by antagonizing the PD-L1/PD-1 interaction
|
Dong, Yujuan
|
|
|
32 |
11 |
p. 4160-4162
|
artikel
|
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