Anti-amyloid treatment is broadly effective in neuronopathic mucopolysaccharidoses and synergizes with gene therapy in MPS-IIIA
Titel:
Anti-amyloid treatment is broadly effective in neuronopathic mucopolysaccharidoses and synergizes with gene therapy in MPS-IIIA
Auteur:
Giaccio, Marianna Monaco, Antonio Galiano, Laura Parente, Andrea Borzacchiello, Luigi Rubino, Riccardo Klärner, Frank-Gerrit Killa, Dennis Perna, Claudia Piccolo, Pasquale Marotta, Marcello Pan, Xuefang Khijniak, Marie Siddique, Ibrar Schrader, Thomas Pshezhetsky, Alexey V. Sorrentino, Nicolina Cristina Bitan, Gal Fraldi, Alessandro