| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV Joins the Rank of Genotoxic Vectors
|
Davé, Utpal P.
|
|
|
29 |
2 |
p. 418-419
|
artikel
|
| 2 |
Anti-tau scFvs Targeted to the Cytoplasm or Secretory Pathway Variably Modify Pathology and Neurodegenerative Phenotypes
|
Goodwin, Marshall S.
|
|
|
29 |
2 |
p. 859-872
|
artikel
|
| 3 |
A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II
|
Okuyama, Torayuki
|
|
|
29 |
2 |
p. 671-679
|
artikel
|
| 4 |
A “Shot in the Arm” for Sickle Cell Disease
|
Townes, Tim M.
|
|
|
29 |
2 |
p. 416-417
|
artikel
|
| 5 |
Autologous CD4 T Lymphocytes Modified with a Tat-Dependent, Virus-Specific Endoribonuclease Gene in HIV-Infected Individuals
|
Jacobson, Jeffrey M.
|
|
|
29 |
2 |
p. 626-635
|
artikel
|
| 6 |
CART19-BE-01: A Multicenter Trial of ARI-0001 Cell Therapy in Patients with CD19+ Relapsed/Refractory Malignancies
|
Ortíz-Maldonado, Valentín
|
|
|
29 |
2 |
p. 636-644
|
artikel
|
| 7 |
Challenges at the Crossroads: Myopathy Trials in 2020 Hindsight
|
Greer, Christopher
|
|
|
29 |
2 |
p. 420-421
|
artikel
|
| 8 |
Clinical Applications of Single-Stranded Oligonucleotides: Current Landscape of Approved and In-Development Therapeutics
|
Scharner, Juergen
|
|
|
29 |
2 |
p. 540-554
|
artikel
|
| 9 |
Clinical CAR-T Cell and Oncolytic Virotherapy for Cancer Treatment
|
Watanabe, Norihiro
|
|
|
29 |
2 |
p. 505-520
|
artikel
|
| 10 |
Clinical Perspective: Treating RPE65-Associated Retinal Dystrophy
|
Maguire, Albert M.
|
|
|
29 |
2 |
p. 442-463
|
artikel
|
| 11 |
Clinical Perspective: Treatment of Aggressive B Cell Lymphomas with FDA-Approved CAR-T Cell Therapies
|
Leick, Mark B.
|
|
|
29 |
2 |
p. 433-441
|
artikel
|
| 12 |
Combinatorial Approaches to Enhance DNA Damage following Enzyme-Mediated Depletion of L-Cys for Treatment of Pancreatic Cancer
|
Saha, Achinto
|
|
|
29 |
2 |
p. 775-787
|
artikel
|
| 13 |
Considerations for Systemic Use of Gene Therapy
|
Byrne, Barry J.
|
|
|
29 |
2 |
p. 422-423
|
artikel
|
| 14 |
CRISPR-Cas9: A Preclinical and Clinical Perspective for the Treatment of Human Diseases
|
Sharma, Garima
|
|
|
29 |
2 |
p. 571-586
|
artikel
|
| 15 |
Current Clinical Applications of In Vivo Gene Therapy with AAVs
|
Mendell, Jerry R.
|
|
|
29 |
2 |
p. 464-488
|
artikel
|
| 16 |
Development of CAR T Cells Expressing a Suicide Gene Plus a Chimeric Antigen Receptor Targeting Signaling Lymphocytic-Activation Molecule F7
|
Amatya, Christina
|
|
|
29 |
2 |
p. 702-717
|
artikel
|
| 17 |
DUX4 Transcript Knockdown with Antisense 2′-O-Methoxyethyl Gapmers for the Treatment of Facioscapulohumeral Muscular Dystrophy
|
Lim, Kenji Rowel Q.
|
|
|
29 |
2 |
p. 848-858
|
artikel
|
| 18 |
Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A
|
Long, Brian R.
|
|
|
29 |
2 |
p. 597-610
|
artikel
|
| 19 |
Efficient Gene Suppression by DNA/DNA Double-Stranded Oligonucleotide In Vivo
|
Asami, Yutaro
|
|
|
29 |
2 |
p. 838-847
|
artikel
|
| 20 |
Engineering Tolerance toward Allogeneic CAR-T Cells by Regulation of MHC Surface Expression with Human Herpes Virus-8 Proteins
|
Wang, Xiaomei
|
|
|
29 |
2 |
p. 718-733
|
artikel
|
| 21 |
Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
|
Li, Yedda
|
|
|
29 |
2 |
p. 691-701
|
artikel
|
| 22 |
First-in-Human Phase I Clinical Trial of an SFV-Based RNA Replicon Cancer Vaccine against HPV-Induced Cancers
|
Komdeur, Fenne L.
|
|
|
29 |
2 |
p. 611-625
|
artikel
|
| 23 |
Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward
|
Choi, Soon H.
|
|
|
29 |
2 |
p. 428-430
|
artikel
|
| 24 |
Immune Responses of Alphavirus Vaccination in Patients with HPV-Induced Cancers
|
Lundstrom, Kenneth
|
|
|
29 |
2 |
p. 415-416
|
artikel
|
| 25 |
In This Issue
|
|
|
|
29 |
2 |
p. 413-414
|
artikel
|
| 26 |
In Vivo HSC Gene Therapy Using a Bi-modular HDAd5/35++ Vector Cures Sickle Cell Disease in a Mouse Model
|
Li, Chang
|
|
|
29 |
2 |
p. 822-837
|
artikel
|
| 27 |
Liver Injury Increases the Incidence of HCC following AAV Gene Therapy in Mice
|
Dalwadi, Dhwanil A.
|
|
|
29 |
2 |
p. 680-690
|
artikel
|
| 28 |
Lost in Translation: Progress and Challenges in Advanced Therapies to Treat CVDs
|
Baker, Andrew H.
|
|
|
29 |
2 |
p. 426-427
|
artikel
|
| 29 |
Monocytic Myeloid-Derived Suppressor Cells Underpin Resistance to Adoptive T Cell Therapy in Nasopharyngeal Carcinoma
|
Hopkins, Richard
|
|
|
29 |
2 |
p. 734-743
|
artikel
|
| 30 |
Neoadjuvant Gene-Mediated Cytotoxic Immunotherapy for Non-Small-Cell Lung Cancer: Safety and Immunologic Activity
|
Predina, Jarrod D.
|
|
|
29 |
2 |
p. 658-670
|
artikel
|
| 31 |
Novel Genetic and Epigenetic Biomarkers of Prognostic and Predictive Significance in Stage II/III Colorectal Cancer
|
Luo, Xiao-Jing
|
|
|
29 |
2 |
p. 587-596
|
artikel
|
| 32 |
Oncolytic Virus Therapy with HSV-1 for Hematological Malignancies
|
Ishino, Ryo
|
|
|
29 |
2 |
p. 762-774
|
artikel
|
| 33 |
Personalized Cancer Vaccines: Clinical Landscape, Challenges, and Opportunities
|
Shemesh, Colby S.
|
|
|
29 |
2 |
p. 555-570
|
artikel
|
| 34 |
Phage Display-Directed Discovery of LEDGF/p75 Binding Cyclic Peptide Inhibitors of HIV Replication
|
Desimmie, Belete A.
|
|
|
29 |
2 |
p. 887
|
artikel
|
| 35 |
Pharmacokinetics and Proceedings in Clinical Application of Nucleic Acid Therapeutics
|
Herkt, Markus
|
|
|
29 |
2 |
p. 521-539
|
artikel
|
| 36 |
RBP EIF2S2 Promotes Tumorigenesis and Progression by Regulating MYC-Mediated Inhibition via FHIT-Related Enhancers
|
Zhang, Jiwei
|
|
|
29 |
2 |
p. 886
|
artikel
|
| 37 |
Regional Hyperthermia Enhances Mesenchymal Stem Cell Recruitment to Tumor Stroma: Implications for Mesenchymal Stem Cell-Based Tumor Therapy
|
Tutter, Mariella
|
|
|
29 |
2 |
p. 788-803
|
artikel
|
| 38 |
Reshaping the Immune Microenvironment by Oncolytic Herpes Simplex Virus in Murine Pancreatic Ductal Adenocarcinoma
|
Zhang, Liming
|
|
|
29 |
2 |
p. 744-761
|
artikel
|
| 39 |
Safety Starts with Selecting the Targets
|
Perna, Fabiana
|
|
|
29 |
2 |
p. 424-425
|
artikel
|
| 40 |
Single-Cell Transcriptomic Analysis Reveals BCMA CAR-T Cell Dynamics in a Patient with Refractory Primary Plasma Cell Leukemia
|
Li, Xue
|
|
|
29 |
2 |
p. 645-657
|
artikel
|
| 41 |
siRNA Drugs: Here to Stay
|
Rossi, John J.
|
|
|
29 |
2 |
p. 431-432
|
artikel
|
| 42 |
Synergistic and Antagonistic Drug Combinations against SARS-CoV-2
|
Bobrowski, Tesia
|
|
|
29 |
2 |
p. 873-885
|
artikel
|
| 43 |
The Chemokine Receptors Ccr5 and Cxcr6 Enhance Migration of Mesenchymal Stem Cells into the Degenerating Retina
|
Pesaresi, Martina
|
|
|
29 |
2 |
p. 804-821
|
artikel
|
| 44 |
Three Decades of Clinical Gene Therapy: From Experimental Technologies to Viable Treatments
|
Tremblay, Jacques P.
|
|
|
29 |
2 |
p. 411-412
|
artikel
|
| 45 |
Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases
|
Tucci, Francesca
|
|
|
29 |
2 |
p. 489-504
|
artikel
|
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