Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
Titel:
Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease
Auteur:
Li, Yedda Miller, Christopher A. Shea, Lauren K. Jiang, Xuntian Guzman, Miguel A. Chandler, Randy J. Ramakrishnan, Sai M. Smith, Stephanie N. Venditti, Charles P. Vogler, Carole A. Ory, Daniel S. Ley, Timothy J. Sands, Mark S.