| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
Adenine base editing reduces misfolded protein accumulation and toxicity in alpha-1 antitrypsin deficient patient iPSC-hepatocytes
|
Werder, Rhiannon B.
|
|
|
29 |
11 |
p. 3219-3229
|
artikel
|
| 2 |
Collaborative science to advance gene therapies in resource-limited parts of the world
|
McCune, Joseph M.
|
|
|
29 |
11 |
p. 3101-3102
|
artikel
|
| 3 |
Co-opting regulation bypass repair as a gene-correction strategy for monogenic diseases
|
Hu, Jingjie
|
|
|
29 |
11 |
p. 3274-3292
|
artikel
|
| 4 |
CRISPR-derived genome editing therapies: Progress from bench to bedside
|
Rees, Holly A.
|
|
|
29 |
11 |
p. 3125-3139
|
artikel
|
| 5 |
CRISPR technologies for the treatment of Duchenne muscular dystrophy
|
Choi, Eunyoung
|
|
|
29 |
11 |
p. 3179-3191
|
artikel
|
| 6 |
Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy
|
Rosanwo, Tolulope O.
|
|
|
29 |
11 |
p. 3163-3178
|
artikel
|
| 7 |
Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy
|
Pickar-Oliver, Adrian
|
|
|
29 |
11 |
p. 3243-3257
|
artikel
|
| 8 |
Gene editing to enhance the efficacy of cancer cell therapies
|
Murty, Tara
|
|
|
29 |
11 |
p. 3153-3162
|
artikel
|
| 9 |
Genome edited B cells: a new frontier in immune cell therapies
|
Rogers, Geoffrey L.
|
|
|
29 |
11 |
p. 3192-3204
|
artikel
|
| 10 |
Genome editing in large animal models
|
Maynard, Lucy H.
|
|
|
29 |
11 |
p. 3140-3152
|
artikel
|
| 11 |
Highly efficient CD4+ T cell targeting and genetic recombination using engineered CD4+ cell-homing mRNA-LNPs
|
Tombácz, István
|
|
|
29 |
11 |
p. 3293-3304
|
artikel
|
| 12 |
Imagine CRISPR cures
|
Urnov, Fyodor D.
|
|
|
29 |
11 |
p. 3103-3106
|
artikel
|
| 13 |
In This Issue
|
|
|
|
29 |
11 |
p. 3095-3096
|
artikel
|
| 14 |
In vivo confusion over in vivo conversion
|
Chen, Gong
|
|
|
29 |
11 |
p. 3097-3098
|
artikel
|
| 15 |
In vivo somatic cell base editing and prime editing
|
Newby, Gregory A.
|
|
|
29 |
11 |
p. 3107-3124
|
artikel
|
| 16 |
RETRACTED: Precise editing of FGFR3-TACC3 fusion genes with CRISPR-Cas13a in glioblastoma
|
Wu, Ye
|
|
|
29 |
11 |
p. 3305-3318
|
artikel
|
| 17 |
Scratching the surface of RGD-directed AAV capsid engineering
|
Zolotukhin, Sergei
|
|
|
29 |
11 |
p. 3099-3100
|
artikel
|
| 18 |
Targeting RNA editing of antizyme inhibitor 1: A potential oligonucleotide-based antisense therapy for cancer
|
Tay, Daryl Jin Tai
|
|
|
29 |
11 |
p. 3258-3273
|
artikel
|
| 19 |
The genome-editing decade
|
Cannon, Paula M.
|
|
|
29 |
11 |
p. 3093-3094
|
artikel
|
| 20 |
Understanding and overcoming adverse consequences of genome editing on hematopoietic stem and progenitor cells
|
Lee, Byung-Chul
|
|
|
29 |
11 |
p. 3205-3218
|
artikel
|
| 21 |
ZFN-mediated in vivo gene editing in hepatocytes leads to supraphysiologic α-Gal A activity and effective substrate reduction in Fabry mice
|
Pagant, Silvere
|
|
|
29 |
11 |
p. 3230-3242
|
artikel
|
Tijdschrift beschrijving