Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy
Titel:
Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy
Auteur:
Pickar-Oliver, Adrian Gough, Veronica Bohning, Joel D. Liu, Siyan Robinson-Hamm, Jacqueline N. Daniels, Heather Majoros, William H. Devlin, Garth Asokan, Aravind Gersbach, Charles A.