| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
ADA-SCID Gene Therapy Endorsed By European Medicines Agency For Marketing Authorization
|
Ylä-Herttuala, Seppo
|
|
2016
|
24 |
6 |
p. 1013-1014
2 p.
|
artikel
|
| 2 |
Allospecific Tregs Expanded After Anergization Remain Suppressive in Inflammatory Conditions but Lack Expression of Gut-homing Molecules
|
Kotsiou, Eleni
|
|
2016
|
24 |
6 |
p. 1126-1134
9 p.
|
artikel
|
| 3 |
CNS-accessible Inhibitor of Glucosylceramide Synthase for Substrate Reduction Therapy of Neuronopathic Gaucher Disease
|
Marshall, John
|
|
2016
|
24 |
6 |
p. 1019-1029
11 p.
|
artikel
|
| 4 |
Corrigendum to “Preclinical Safety and Efficacy of Human CD34+ Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome”
|
|
|
2016
|
24 |
6 |
p. 1159-
1 p.
|
artikel
|
| 5 |
Corrigendum to “T-cell Subsets in Peripheral Blood and Tumors of Patients Treated With Oncolytic Adenoviruses”
|
|
|
2016
|
24 |
6 |
p. 1159-
1 p.
|
artikel
|
| 6 |
Engineering Periodic shRNA for Enhanced Silencing Efficacy
|
Wu, Connie
|
|
2016
|
24 |
6 |
p. 1070-1077
8 p.
|
artikel
|
| 7 |
Evaluating the Safety of Retroviral Vectors Based on Insertional Oncogene Activation and Blocked Differentiation in Cultured Thymocytes
|
Zhou, Sheng
|
|
2016
|
24 |
6 |
p. 1090-1099
10 p.
|
artikel
|
| 8 |
GD2-specific CAR T Cells Undergo Potent Activation and Deletion Following Antigen Encounter but can be Protected From Activation-induced Cell Death by PD-1 Blockade
|
Gargett, Tessa
|
|
2016
|
24 |
6 |
p. 1135-1149
15 p.
|
artikel
|
| 9 |
Genetic Manipulation of Brown Fat Via Oral Administration of an Engineered Recombinant Adeno-associated Viral Serotype Vector
|
Huang, Wei
|
|
2016
|
24 |
6 |
p. 1062-1069
8 p.
|
artikel
|
| 10 |
In This Issue
|
|
|
2016
|
24 |
6 |
p. 1015-
1 p.
|
artikel
|
| 11 |
Protein Kinase C-α is a Critical Protein for Antisense Oligonucleotide-mediated Silencing in Mammalian Cells
|
Castanotto, Daniela
|
|
2016
|
24 |
6 |
p. 1117-1125
9 p.
|
artikel
|
| 12 |
Pulmonary Targeting of Adeno-associated Viral Vectors by Next-generation Sequencing-guided Screening of Random Capsid Displayed Peptide Libraries
|
Körbelin, Jakob
|
|
2016
|
24 |
6 |
p. 1050-1061
12 p.
|
artikel
|
| 13 |
rAAV Gene Therapy in a Canavan's Disease Mouse Model Reveals Immune Impairments and an Extended Pathology Beyond the Central Nervous System
|
Ahmed, Seemin Seher
|
|
2016
|
24 |
6 |
p. 1030-1041
12 p.
|
artikel
|
| 14 |
Randomized Phase 2 Trial of the Oncolytic Virus Pelareorep (Reolysin) in Upfront Treatment of Metastatic Pancreatic Adenocarcinoma
|
Noonan, Anne M
|
|
2016
|
24 |
6 |
p. 1150-1158
9 p.
|
artikel
|
| 15 |
Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients
|
Gil-Farina, Irene
|
|
2016
|
24 |
6 |
p. 1100-1105
6 p.
|
artikel
|
| 16 |
Research Highlights
|
|
|
2016
|
24 |
6 |
p. 1016-
1 p.
|
artikel
|
| 17 |
Stable, Nonviral Expression of Mutated Tumor Neoantigen-specific T-cell Receptors Using the Sleeping Beauty Transposon/Transposase System
|
Deniger, Drew C
|
|
2016
|
24 |
6 |
p. 1078-1089
12 p.
|
artikel
|
| 18 |
Superior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid
|
Vercauteren, Koen
|
|
2016
|
24 |
6 |
p. 1042-1049
8 p.
|
artikel
|
| 19 |
Targeted Delivery of C/EBPα -saRNA by Pancreatic Ductal Adenocarcinoma-specific RNA Aptamers Inhibits Tumor Growth In Vivo
|
Yoon, Sorah
|
|
2016
|
24 |
6 |
p. 1106-1116
11 p.
|
artikel
|
| 20 |
Timing of Gene Therapy Interventions: The Earlier, the Better
|
Gray, Steven J
|
|
2016
|
24 |
6 |
p. 1017-1018
2 p.
|
artikel
|
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