CNS-accessible Inhibitor of Glucosylceramide Synthase for Substrate Reduction Therapy of Neuronopathic Gaucher Disease
Titel:
CNS-accessible Inhibitor of Glucosylceramide Synthase for Substrate Reduction Therapy of Neuronopathic Gaucher Disease
Auteur:
Marshall, John Sun, Ying Bangari, Dinesh S Budman, Eva Park, Hyejung Nietupski, Jennifer B Allaire, Amy Cromwell, Mary A Wang, Bing Grabowski, Gregory A Leonard, John P Cheng, Seng H
Verschenen in:
Molecular therapy
Paginering:
Jaargang 24 (2016) nr. 6 pagina's 11 p.
Jaar:
2016
Inhoud:
Uitgever:
Official journal of the American Society of Gene & Cell Therapy