| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A 10376 bp deletion of FECH gene responsible for erythropoietic protoporphyria
|
Di Pierro, Elena
|
|
2008
|
40 |
2 |
p. 233-236
4 p.
|
artikel
|
| 2 |
A case report of 5 Japanese patients who received infusions of HSV-TK transduced donor lymphocytes for relapsed leukemia after allo-stem cell transplantation
|
Onodera, Masafumi
|
|
2008
|
40 |
2 |
p. 279-
1 p.
|
artikel
|
| 3 |
A comparative analysis of the leukemic potential of mature T cells versus T cell precursors
|
Newrzela, Sebastian
|
|
2008
|
40 |
2 |
p. 290-291
2 p.
|
artikel
|
| 4 |
A critical role for Smad4 in the self-renewal of hematopoietic stem cells
|
Karlsson, Göran
|
|
2008
|
40 |
2 |
p. 271-
1 p.
|
artikel
|
| 5 |
A dual activation mechanism for Myb-responsive genes in myelomonocytic cells
|
Yamkamon, Vichanan
|
|
2008
|
40 |
2 |
p. 219-226
8 p.
|
artikel
|
| 6 |
Alloantigenic reactions after hematopoietic cell transplantation induce genomic alterations in epithelial cells
|
Themeli, M.
|
|
2008
|
40 |
2 |
p. 287-
1 p.
|
artikel
|
| 7 |
A mobilization study for major β-thalassemia
|
Yannaki, Evangelia
|
|
2008
|
40 |
2 |
p. 293-294
2 p.
|
artikel
|
| 8 |
A mobilization study in the thalassemic mouse model: Implications for human gene therapy of thalassemia
|
Yannaki, Evangelia
|
|
2008
|
40 |
2 |
p. 281-282
2 p.
|
artikel
|
| 9 |
Appropriate conditioning regimens for clinical gene therapy
|
Fassas, Athanasios
|
|
2008
|
40 |
2 |
p. 265-266
2 p.
|
artikel
|
| 10 |
Bicistronic vectors for adoptive immunotherapy in pediatric leukemia patients
|
Vogler, Isabel
|
|
2008
|
40 |
2 |
p. 289-
1 p.
|
artikel
|
| 11 |
Bone marrow-derived mesenchymal stromal cells (MSCs) as efficient in vivo cellular vehicles for plasma soluble protein delivery
|
Eliopoulos, Nicoletta
|
|
2008
|
40 |
2 |
p. 263-264
2 p.
|
artikel
|
| 12 |
Cancer stem cells: New therapeutic targets?
|
Bonnet, Dominique
|
|
2008
|
40 |
2 |
p. 256-
1 p.
|
artikel
|
| 13 |
Comparative integration site profile analysis in 5 clinical retroviral gene therapy studies
|
Deichman, Annette
|
|
2008
|
40 |
2 |
p. 262-
1 p.
|
artikel
|
| 14 |
Comparative study of different promoters driving eGFP for use in episomal gene transfer in CD34+ cells
|
Stavrou, E.F.
|
|
2008
|
40 |
2 |
p. 286-287
2 p.
|
artikel
|
| 15 |
Detailed studies on the mechanism and factors mediating lipofection potency of cationic phosphonolipid-based gene transfer into human cells
|
Koumbi, D.
|
|
2008
|
40 |
2 |
p. 272-273
2 p.
|
artikel
|
| 16 |
Determination of the profile and site preference of lentiviral vector integration in primary astrocyte cultures
|
Hacker, C.V.
|
|
2008
|
40 |
2 |
p. 269-
1 p.
|
artikel
|
| 17 |
Development of effective and safe lentiviral vectors for the treatment of X-linked severe combined immunodeficiency
|
Zhou, Sheng
|
|
2008
|
40 |
2 |
p. 285-
1 p.
|
artikel
|
| 18 |
Development of foamy virus vectors for the genetic correction of beta-thalassemia
|
Morianos, John
|
|
2008
|
40 |
2 |
p. 277-278
2 p.
|
artikel
|
| 19 |
Disturbance in the HIF-1α pathway associated with erythrocytosis: Further evidences brought by frameshift and nonsense mutations in the prolyl hydroxylase domain protein 2 (PHD2) gene
|
Al-Sheikh, Maha
|
|
2008
|
40 |
2 |
p. 160-165
6 p.
|
artikel
|
| 20 |
DNA repair: An essential role in stem cell maintenance
|
Gerson, S.L.
|
|
2008
|
40 |
2 |
p. 267-268
2 p.
|
artikel
|
| 21 |
Editorial Board
|
|
|
2008
|
40 |
2 |
p. IFC-
1 p.
|
artikel
|
| 22 |
Effective gene therapy of congenital erythropoietic porphyria mice improved by a survival advantage of corrected cells
|
Robert-Richard, Elodie
|
|
2008
|
40 |
2 |
p. 277-
1 p.
|
artikel
|
| 23 |
E-infrastructure for Thalassemia Research Network (Ithanet)
|
Kleanthous, Marina
|
|
2008
|
40 |
2 |
p. 272-
1 p.
|
artikel
|
| 24 |
Elements of cHS4 insulator necessary for maximum chromatin barrier activity
|
Arumugam, Paritha
|
|
2008
|
40 |
2 |
p. 252-
1 p.
|
artikel
|
| 25 |
Epigenetic analysis of the human α- and β-globin gene clusters
|
Fathallah, Hassana
|
|
2008
|
40 |
2 |
p. 166-173
8 p.
|
artikel
|
| 26 |
Erythroid differentiation and maturation from peripheral CD34+ cells in liquid culture: Cellular and molecular characterization
|
Ronzoni, Luisa
|
|
2008
|
40 |
2 |
p. 148-155
8 p.
|
artikel
|
| 27 |
Evidence for efficacy and safety of lentiviral mediated gene transfer in Wiskott–Aldrich syndrome
|
Grazia Roncarolo, Maria Grazia
|
|
2008
|
40 |
2 |
p. 282-
1 p.
|
artikel
|
| 28 |
Excellent retroviral transduction efficiency achieved with GMP grade American fluoroseal bags, comparable to tissue culture plates or Nexell X-fold bags
|
Becker, P.S.
|
|
2008
|
40 |
2 |
p. 254-255
2 p.
|
artikel
|
| 29 |
Exploiting microRNA expression profiles for lineage- and differentiation state-specific transgene expression in hematopoietic, neural and embryonic stem cells
|
Gentner, Bernhard
|
|
2008
|
40 |
2 |
p. 267-
1 p.
|
artikel
|
| 30 |
Ex vivo expansion of hematopoietic stem cells for use in nonmyeloablative transplantation
|
Bakovic, S.
|
|
2008
|
40 |
2 |
p. 269-270
2 p.
|
artikel
|
| 31 |
Full-length cDNA cloning and protein three-dimensional structure modeling of factor VII of rhesus monkey, Macaca mulatta
|
Wang, Jiandong
|
|
2008
|
40 |
2 |
p. 237-243
7 p.
|
artikel
|
| 32 |
Gamma-globin lentiviral vector-mediated stem cell gene therapy of beta-thalassemia and sickle cell disease
|
Zhao, Huifen
|
|
2008
|
40 |
2 |
p. 281-
1 p.
|
artikel
|
| 33 |
Gammaretroviral vector integration preference for DNAse hypersensitive sites
|
Liu, Mingdong
|
|
2008
|
40 |
2 |
p. 264-
1 p.
|
artikel
|
| 34 |
Gatekeeper function of the RUNX1 transcription factor in acute leukemia
|
Niebuhr, Birte
|
|
2008
|
40 |
2 |
p. 211-218
8 p.
|
artikel
|
| 35 |
Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery
|
Lombardo, A.
|
|
2008
|
40 |
2 |
p. 278-
1 p.
|
artikel
|
| 36 |
Gene therapy for adenosine deaminase deficiency in the USA
|
Condotti, Fabio
|
|
2008
|
40 |
2 |
p. 258-259
2 p.
|
artikel
|
| 37 |
Gene therapy for HIV-infection: Preclinical and clinical studies
|
Kimpel, Janine
|
|
2008
|
40 |
2 |
p. 290-
1 p.
|
artikel
|
| 38 |
Gene therapy targeting hematopoietic stem cells: From the bench to the bedside
|
Cavazzana-Calvo, M.
|
|
2008
|
40 |
2 |
p. 259-
1 p.
|
artikel
|
| 39 |
Genotoxicity in the rhesus macaque model
|
Dunbar, Cynthia E.
|
|
2008
|
40 |
2 |
p. 263-
1 p.
|
artikel
|
| 40 |
Hematologically important mutations: Shwachman–Diamond syndrome
|
Costa, Elísio
|
|
2008
|
40 |
2 |
p. 183-184
2 p.
|
artikel
|
| 41 |
Hematopoietic stem cell gene therapy for ADA-SCID
|
Aiuti, Alessandro
|
|
2008
|
40 |
2 |
p. 248-250
3 p.
|
artikel
|
| 42 |
Hematopoietic stem cell gene therapy for inherited platelet bleeding disorders
|
Wilcox, David A.
|
|
2008
|
40 |
2 |
p. 291-
1 p.
|
artikel
|
| 43 |
Hematopoietic stem cell gene transfer and expansion/selection studies in large animal models
|
Kiem, Hans-Peter
|
|
2008
|
40 |
2 |
p. 271-
1 p.
|
artikel
|
| 44 |
Hematopoietic stem cell (HSC) gene therapy for two patients with adenosine deaminase (ADA) deficiency without cytoreductive conditioning; a suggestion for the optimal protocol for HSC gene therapy for ADA deficiency
|
Ariga, Tadashi
|
|
2008
|
40 |
2 |
p. 251-
1 p.
|
artikel
|
| 45 |
Identification and functional characterization of novel telomerase variant alleles in Japanese patients with bone-marrow failure syndromes
|
Takeuchi, Junko
|
|
2008
|
40 |
2 |
p. 185-191
7 p.
|
artikel
|
| 46 |
Impact of lipoplex physicochemical properties upon transgene incorporation, stability and mode of nuclear targeting in cationic phosphonolipid- and lipophosphoramide-mediated transfection into human cells
|
Koumbi, D.
|
|
2008
|
40 |
2 |
p. 273-
1 p.
|
artikel
|
| 47 |
Induction of fetal hemoglobin (HbF) by novel alkylating agents in human erythroid cells; synergistic effects with established HbF-inducing agents
|
Chiotoglou, I.
|
|
2008
|
40 |
2 |
p. 260-261
2 p.
|
artikel
|
| 48 |
Infusion of suicide gene-modified donor T cells promotes a rapid and effective immune reconstitution and provides long-term survival after haploidentical hemaopoietic cell transplantation for the cure of patients with high-risk leukemia
|
Bonini, C.
|
|
2008
|
40 |
2 |
p. 286-
1 p.
|
artikel
|
| 49 |
Initial evaluation of oncoretroviral vectors carrying HIV-1 inhibitor gene into rhesus CD34+ cells and/or CD4+ T cells: An in vivo model for the gene therapy of AIDS
|
Braun, Stephen E.
|
|
2008
|
40 |
2 |
p. 257-
1 p.
|
artikel
|
| 50 |
Insights from clinical studies into the role of the MLL gene in infant and childhood leukemia
|
Chowdhury, Tanzina
|
|
2008
|
40 |
2 |
p. 192-199
8 p.
|
artikel
|
| 51 |
Interactions between retroviral vectors and the genome of CD34+ hematopoietic cells
|
Mavilio, Fulvio
|
|
2008
|
40 |
2 |
p. 276-
1 p.
|
artikel
|
| 52 |
In vivo gene transfer to hematopoietic and mesenchymal stromal cells by lentiviral vector
|
Nifontova, Irina
|
|
2008
|
40 |
2 |
p. 278-
1 p.
|
artikel
|
| 53 |
Lentivirus vectors for gene therapy for hemoglobinopathies
|
Arumugam, Paritha
|
|
2008
|
40 |
2 |
p. 275-276
2 p.
|
artikel
|
| 54 |
Long-term efficacy and safety of hematopoietic stem cell gene therapy mediated by lentiviral vectors in the murine model of Wiskott-Aldrich syndrome
|
Bosticardo, Marita
|
|
2008
|
40 |
2 |
p. 256-257
2 p.
|
artikel
|
| 55 |
Mesenchymal cell targeting by TNF as a common pathogenic principle in chronic inflammatory joint and intestinal diseases
|
Armaka, Maria
|
|
2008
|
40 |
2 |
p. 251-252
2 p.
|
artikel
|
| 56 |
MicroRNA regulation directs lineage- and developmental stage-specific transgene expression in hematopoietic stem cell progeny
|
Papapetrou, Eirini
|
|
2008
|
40 |
2 |
p. 280-
1 p.
|
artikel
|
| 57 |
Modeling the genotoxicity of viral vector integration in a tumor prone hematopoietic stem cell transplantation model
|
Montini, Eugenio
|
|
2008
|
40 |
2 |
p. 276-277
2 p.
|
artikel
|
| 58 |
Modulation of homing/engraftment of ex vivo incubated HSCs and putative corrective strategies
|
Papayannopoulou, Thalia
|
|
2008
|
40 |
2 |
p. 280-281
2 p.
|
artikel
|
| 59 |
Molecular mechanisms of NPC-mediated repair of autoimmune demyelination
|
Denis, Maria C.
|
|
2008
|
40 |
2 |
p. 262-263
2 p.
|
artikel
|
| 60 |
Multiple infusions of G-CSF-mobilized peripheral blood stem cells can reverse the clinical course of decompensated alcoholic cirrhosis
|
Yannaki, Evangelia
|
|
2008
|
40 |
2 |
p. 293-
1 p.
|
artikel
|
| 61 |
Natural gene therapy: Somatic reversion in the Wiskott–Aldrich syndrome
|
Davis, Brian R.
|
|
2008
|
40 |
2 |
p. 261-
1 p.
|
artikel
|
| 62 |
Nearly random integration site distribution in postmitotic rodent tissues transduced with lentiviral SIN-vectors
|
Bartholomae, Cynthia C.
|
|
2008
|
40 |
2 |
p. 253-
1 p.
|
artikel
|
| 63 |
Non-coding transcript in T cells (NTT): Antisense transcript activates PKR and NF-κB in human lymphocytes
|
Delgado André, Nayara
|
|
2008
|
40 |
2 |
p. 227-232
6 p.
|
artikel
|
| 64 |
Novel insulated gamma globin SIN lentiviral vectors with the HPFH-2 enhancer and the − 117 HPFH active promoter efficiently transducer thalassemic CD34+ cells and prevent their apoptosis
|
Papanikolau, Eleni
|
|
2008
|
40 |
2 |
p. 279-280
2 p.
|
artikel
|
| 65 |
Novel lentivirus vectors for safe and efficient gene therapy of hemoglobin disorders
|
Bodine, David
|
|
2008
|
40 |
2 |
p. 255-
1 p.
|
artikel
|
| 66 |
Optimization of lentiviral vectors for the gene therapy of fanconi anemia
|
Gonzalez-Murillo, Africa
|
|
2008
|
40 |
2 |
p. 268-
1 p.
|
artikel
|
| 67 |
Optimization of the beta-globin LCR and promoter elements for lentiviral vector-encoded the beta-globin transgene expression in beta-thalassemic mice
|
Lisowski, Leszek
|
|
2008
|
40 |
2 |
p. 274-
1 p.
|
artikel
|
| 68 |
Phase I/II gene therapy study for X-CGD: Results, lessons and perspectives
|
Grez, Manuel
|
|
2008
|
40 |
2 |
p. 268-269
2 p.
|
artikel
|
| 69 |
Preclinical assessment of gene therapy for beta thalassemia
|
Ferrari, Giuliana
|
|
2008
|
40 |
2 |
p. 266-
1 p.
|
artikel
|
| 70 |
Preclinical gene therapy studies of fanconi anemia with lentiviral vectors
|
Jacome, A.
|
|
2008
|
40 |
2 |
p. 258-
1 p.
|
artikel
|
| 71 |
Random and targeted integration of adeno-associated virus vectors
|
Russel, David W.
|
|
2008
|
40 |
2 |
p. 282-283
2 p.
|
artikel
|
| 72 |
Rapid screening of 10 common mutations in Turkish Gaucher patients using electronic DNA microarray
|
Ezgu, Fatih
|
|
2008
|
40 |
2 |
p. 246-247
2 p.
|
artikel
|
| 73 |
Reconstitution of immune function in adenosine deaminase deficient severe combined immunodeficiency following hematopoietic stem cell gene therapy
|
Gaspar, H. Bobby
|
|
2008
|
40 |
2 |
p. 266-267
2 p.
|
artikel
|
| 74 |
Red blood cells as a physiological source of glutathione for extracellular fluids
|
Giustarini, Daniela
|
|
2008
|
40 |
2 |
p. 174-179
6 p.
|
artikel
|
| 75 |
Reducing retroviral vector genotoxicity with chromatin insulators
|
Emery, David W.
|
|
2008
|
40 |
2 |
p. 264-265
2 p.
|
artikel
|
| 76 |
Requirements for retroviral targeting of a suicide gene to alloreactive memory stem T cells for adoptive immunotherapy of leukemia
|
Bondanza, A.
|
|
2008
|
40 |
2 |
p. 255-256
2 p.
|
artikel
|
| 77 |
Resveratrol, a natural antioxidant phytoalexin, and 4 synthetic derivatives can promote expression of gamma-globin gene in vitro
|
Spyrou, Pandelis
|
|
2008
|
40 |
2 |
p. 271-272
2 p.
|
artikel
|
| 78 |
Retroviral transgenesis and oncogenesis
|
Baum, Christopher
|
|
2008
|
40 |
2 |
p. 253-254
2 p.
|
artikel
|
| 79 |
Significant increase of self-renewal in hematopoietic cells after forced expression of EVI1
|
Laricchia-Robbio, Leopoldo
|
|
2008
|
40 |
2 |
p. 141-147
7 p.
|
artikel
|
| 80 |
Silencing of proviral transgene expression by CpG methylation in a gene therapy trial for chronic granulomatous disease
|
Schultze-Strasser, Stephan
|
|
2008
|
40 |
2 |
p. 283-284
2 p.
|
artikel
|
| 81 |
SIN gammaretroviral vectors for the gene therapy of x-CGD
|
Chen-Wichmann, Linping
|
|
2008
|
40 |
2 |
p. 260-
1 p.
|
artikel
|
| 82 |
Stem cell gene transfer with foamy virus vectors
|
Vassilopoulos, G.
|
|
2008
|
40 |
2 |
p. 288-289
2 p.
|
artikel
|
| 83 |
Successful bone marrow gene therapy for SCID
|
Trasher, Adrian J
|
|
2008
|
40 |
2 |
p. 287-288
2 p.
|
artikel
|
| 84 |
Successful gene therapy of canine leukocyte adhesion deficiency using foamy viral vectors
|
Bauer, Thomas R.
|
|
2008
|
40 |
2 |
p. 269-
1 p.
|
artikel
|
| 85 |
Targeted integration of adenovirus vectors in hematopoietic stem cells
|
Wang, Hongjie
|
|
2008
|
40 |
2 |
p. 273-274
2 p.
|
artikel
|
| 86 |
The clonal fate of gene corrected myelo- and lymphopoiesis
|
Schmidt, Manfred
|
|
2008
|
40 |
2 |
p. 289-290
2 p.
|
artikel
|
| 87 |
The gene corrected clonal inventory in clinical gene therapy trials
|
Schwarzwaelder, Kerstin
|
|
2008
|
40 |
2 |
p. 284-
1 p.
|
artikel
|
| 88 |
The high oxygen-affinity Hemoglobin Johnstown [(β109(G11) Val→Leu] in a German kindred with an elevated erythrocyte hemoglobin content: Potential interaction with HFE mutations
|
Petrides, Petro E.
|
|
2008
|
40 |
2 |
p. 180-182
3 p.
|
artikel
|
| 89 |
The MTHFR polymorphism C677T in adult patients with acute lymphoblastic leukemia is associated with an increased prevalence of cytogenetic abnormalities
|
Gallegos-Arreola, M.P.
|
|
2008
|
40 |
2 |
p. 244-245
2 p.
|
artikel
|
| 90 |
The role of the vav promoter in gene therapy: Safer vectors with weaker and stable expression
|
Almarza, Elena
|
|
2008
|
40 |
2 |
p. 250-251
2 p.
|
artikel
|
| 91 |
Too little, too late: The initial experience in FA gene therapy
|
Milsom, Michael D.
|
|
2008
|
40 |
2 |
p. 291-292
2 p.
|
artikel
|
| 92 |
Too much of a good thing? MGMT in chemoresistance and brain tumor therapy
|
Milsom, Michael D.
|
|
2008
|
40 |
2 |
p. 292-293
2 p.
|
artikel
|
| 93 |
Transcriptional and post transcriptional gene regulation in stem cell-based gene therapy
|
Sadelain, Michel
|
|
2008
|
40 |
2 |
p. 283-
1 p.
|
artikel
|
| 94 |
Transcriptional complexity of the HOXA9 locus
|
Popovic, Relja
|
|
2008
|
40 |
2 |
p. 156-159
4 p.
|
artikel
|
| 95 |
Transduction of human and murine hematopoietic progenitors with a lentiviral vector for fanconi anemia complementation group A
|
Becker, P.S.
|
|
2008
|
40 |
2 |
p. 254-
1 p.
|
artikel
|
| 96 |
Transient expression of AAV rep protein facilitates targeted integration of a 200 kb BAC containing the entire beta-globin locus
|
Howden, S.E.
|
|
2008
|
40 |
2 |
p. 288-
1 p.
|
artikel
|
| 97 |
Transplantation of hematopoietic stem cells encoding a high-expression factor VIII transgene under myeloablative and nonmyeloablative conditioning provides curative factor VIII activity to hemophilia A mice
|
Doering, Christopher B.
|
|
2008
|
40 |
2 |
p. 285-286
2 p.
|
artikel
|
| 98 |
Treatment of infections in patients with X-linked chronic granulomatous disease (CGD) with gene therapy
|
Kang, Elizabeth M.
|
|
2008
|
40 |
2 |
p. 270-271
2 p.
|
artikel
|
| 99 |
Ubiquitin-mediated proteasomal degradation in normal and malignant hematopoiesis
|
Heuzé, Mélina L.
|
|
2008
|
40 |
2 |
p. 200-210
11 p.
|
artikel
|
| 100 |
UCOE (ubiquitous chromatin opening element) mediates copy dependent expression of gp91phox in lentiviral vectors
|
Brendel, Christian
|
|
2008
|
40 |
2 |
p. 257-258
2 p.
|
artikel
|
| 101 |
Update on gene therapy for Chronic Granulomatous Disease: Current studies and future approaches
|
Malech, Harry L.
|
|
2008
|
40 |
2 |
p. 274-275
2 p.
|
artikel
|
| 102 |
WASP-deficient hematopoietic progenitor cells mobilize in response to G-CSF and can restore hematopoiesis in mice
|
Charrier, Sabine
|
|
2008
|
40 |
2 |
p. 259-260
2 p.
|
artikel
|
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