Evidence for efficacy and safety of lentiviral mediated gene transfer in Wiskott–Aldrich syndrome
Titel:
Evidence for efficacy and safety of lentiviral mediated gene transfer in Wiskott–Aldrich syndrome
Auteur:
Grazia Roncarolo, Maria Grazia Bosticardo, Marita Marangoni, Francesco Scaramuzza, Samantha Trifari, Sara Galy, Anne Dupré, Loïc Naldini, Luigi Aiuti, Alessandro Villa, Anna