Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification
Titel:
Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification
Auteur:
Chan, Amy Liebow, Abigail Yasuda, Makiko Gan, Lin Racie, Tim Maier, Martin Kuchimanchi, Satya Foster, Don Milstein, Stuart Charisse, Klaus Sehgal, Alfica Manoharan, Muthiah Meyers, Rachel Fitzgerald, Kevin Simon, Amy Desnick, Robert J Querbes, William
Verschenen in:
Molecular therapy - nucleic acids
Paginering:
Jaargang 4 (2015) nr. C pagina's 1 p.
Jaar:
2015
Inhoud:
Uitgever:
Official journal of the American Society of Gene & Cell Therapy