Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification
Title:
Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification
Author:
Chan, Amy Liebow, Abigail Yasuda, Makiko Gan, Lin Racie, Tim Maier, Martin Kuchimanchi, Satya Foster, Don Milstein, Stuart Charisse, Klaus Sehgal, Alfica Manoharan, Muthiah Meyers, Rachel Fitzgerald, Kevin Simon, Amy Desnick, Robert J Querbes, William
Appeared in:
Molecular therapy - nucleic acids
Paging:
Volume 4 (2015) nr. C pages 1 p.
Year:
2015
Contents:
Publisher:
Official journal of the American Society of Gene & Cell Therapy