Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Titel:
Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Auteur:
Sinha, Divya Steyer, Benjamin Shahi, Pawan K. Mueller, Katherine P. Valiauga, Rasa Edwards, Kimberly L. Bacig, Cole Steltzer, Stephanie S. Srinivasan, Sandhya Abdeen, Amr Cory, Evan Periyasamy, Viswesh Siahpirani, Alireza Fotuhi Stone, Edwin M. Tucker, Budd A. Roy, Sushmita Pattnaik, Bikash R. Saha, Krishanu Gamm, David M.