Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Title:
Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Author:
Sinha, Divya Steyer, Benjamin Shahi, Pawan K. Mueller, Katherine P. Valiauga, Rasa Edwards, Kimberly L. Bacig, Cole Steltzer, Stephanie S. Srinivasan, Sandhya Abdeen, Amr Cory, Evan Periyasamy, Viswesh Siahpirani, Alireza Fotuhi Stone, Edwin M. Tucker, Budd A. Roy, Sushmita Pattnaik, Bikash R. Saha, Krishanu Gamm, David M.