NCALD Antisense Oligonucleotide Therapy in Addition to Nusinersen further Ameliorates Spinal Muscular Atrophy in Mice
Titel:
NCALD Antisense Oligonucleotide Therapy in Addition to Nusinersen further Ameliorates Spinal Muscular Atrophy in Mice
Auteur:
Torres-Benito, Laura Schneider, Svenja Rombo, Roman Ling, Karen K. Grysko, Vanessa Upadhyay, Aaradhita Kononenko, Natalia L. Rigo, Frank Bennett, C. Frank Wirth, Brunhilde