|
A high-fidelity RNA-targeting Cas13 restores paternal Ube3a expression and improves motor functions in Angelman syndrome mice |
|
|
|
Titel: |
A high-fidelity RNA-targeting Cas13 restores paternal Ube3a expression and improves motor functions in Angelman syndrome mice |
Auteur: |
Li, Jinhui Shen, Zhixin Liu, Yajing Yan, Zixiang Liu, Yuanhua Lin, Xiang Tang, Junjie Lv, Ruimin Geng, Guannan Xiong, Zhi-Qi Zhou, Changyang Yang, Hui |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 31 () nr. 7 pagina's 2286-2295 |
Jaar: |
2023 |
Inhoud: |
|
Uitgever: |
The American Society of Gene and Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
|
|
|
|