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A high-fidelity RNA-targeting Cas13 restores paternal Ube3a expression and improves motor functions in Angelman syndrome mice |
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Title: |
A high-fidelity RNA-targeting Cas13 restores paternal Ube3a expression and improves motor functions in Angelman syndrome mice |
Author: |
Li, Jinhui Shen, Zhixin Liu, Yajing Yan, Zixiang Liu, Yuanhua Lin, Xiang Tang, Junjie Lv, Ruimin Geng, Guannan Xiong, Zhi-Qi Zhou, Changyang Yang, Hui |
Appeared in: |
Molecular therapy |
Paging: |
Volume 31 () nr. 7 pages 2286-2295 |
Year: |
2023 |
Contents: |
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Publisher: |
The American Society of Gene and Cell Therapy |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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