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A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis |
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Titel: |
A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis |
Auteur: |
Takai, Tomoko Higaki, Katsumi Aguilar-Moncayo, Matilde Mena-Barragán, Teresa Hirano, Yuki Yura, Kei Yu, Liang Ninomiya, Haruaki García-Moreno, M. Isabel Sakakibara, Yasubumi Ohno, Kousaku Nanba, Eiji Ortiz Mellet, Carmen García Fernández, José M. Suzuki, Yoshiyuki |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 21 (2013) nr. 3 pagina's 7 p. |
Jaar: |
2013 |
Inhoud: |
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Uitgever: |
The American Society of Gene & Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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