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A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis |
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Title: |
A Bicyclic 1-Deoxygalactonojirimycin Derivative as a Novel Pharmacological Chaperone for GM1 Gangliosidosis |
Author: |
Takai, Tomoko Higaki, Katsumi Aguilar-Moncayo, Matilde Mena-Barragán, Teresa Hirano, Yuki Yura, Kei Yu, Liang Ninomiya, Haruaki García-Moreno, M. Isabel Sakakibara, Yasubumi Ohno, Kousaku Nanba, Eiji Ortiz Mellet, Carmen García Fernández, José M. Suzuki, Yoshiyuki |
Appeared in: |
Molecular therapy |
Paging: |
Volume 21 (2013) nr. 3 pages 7 p. |
Year: |
2013 |
Contents: |
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Publisher: |
The American Society of Gene & Cell Therapy |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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